Potential mechanisms for cell-based gene therapy to treat HIV/AIDS

[Introduction] An estimated 35 million people are infected with HIV worldwide. Anti-retroviral therapy (ART) has reduced the morbidity and mortality of HIV-infected patients but efficacy requires strict adherence and the treatment is not curative. Most importantly, the emergence of drug-resistant vi...

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Detalles Bibliográficos
Autores: Herrera, Elena, Berkhout, Ben
Tipo de recurso: artículo
Estado:Versión enviada para evaluación y publicación
Fecha de publicación:2015
País:España
Institución:Consejo Superior de Investigaciones Científicas (CSIC)
Repositorio:DIGITAL.CSIC. Repositorio Institucional del CSIC
OAI Identifier:oai:digital.csic.es:10261/415474
Acceso en línea:http://hdl.handle.net/10261/415474
https://api.elsevier.com/content/abstract/scopus_id/84921294877
Access Level:acceso abierto
Palabra clave:HIV-1
RNA decoy
RNA interference
Antisense
Antiviral
Gene therapy
Hematopoietic stem cell
Intracellular immunization
Nuclease
Ribozyme
Trans-dominant negative mutant
Descripción
Sumario:[Introduction] An estimated 35 million people are infected with HIV worldwide. Anti-retroviral therapy (ART) has reduced the morbidity and mortality of HIV-infected patients but efficacy requires strict adherence and the treatment is not curative. Most importantly, the emergence of drug-resistant virus strains and drug toxicity can restrict the long-term therapeutic efficacy in some patients. Therefore, novel treatment strategies that permanently control or eliminate the virus and restore the damaged immune system are required. Gene therapy against HIV infection has been the topic of intense investigations for the last two decades because it can theoretically provide such a durable anti-HIV control.