Novel mutations in the ferritin-L iron-responsive element that only mildly impair IRP binding cause hereditary hyperferritinaemia cataract syndrome

This work was supported by the grant PS09/00341 from “Instituto de Salud Carlos III”, Spanish Health Program, grant SAF2012-40106 from Ministry of Economy and Competitiveness (MINECO) and grant CIVP16A1857 “Ayudas a proyectos de Investigación en Ciéncias de la Vida Fundación Ramón Areces” to M.S. M....

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Detalles Bibliográficos
Autores: Luscieti, Sara, Tolle, Gabriele, Aranda, Jessica, Benet Campos, Carmen, Risse, Frank, Morán, Érica, Muckenthaler, Martina U., Sanchez-Fernandez, Mayka
Tipo de recurso: artículo
Fecha de publicación:2013
País:España
Institución:Varias* (Consorci de Biblioteques Universitáries de Catalunya, Centre de Serveis Científics i Acadèmics de Catalunya)
Repositorio:Recercat. Dipósit de la Recerca de Catalunya
OAI Identifier:oai:recercat.cat:20.500.12328/3079
Acceso en línea:http://hdl.handle.net/20.500.12328/3079
https://dx.doi.org/10.1186/1750-1172-8-30
Access Level:acceso abierto
Palabra clave:Mutacions
Ferro ferritina-L
Síndrome de cataracta d'hiperferritinèmia hereditària
Ferritina sèrica
Metabolisme del ferro
Sistema regulador IRP/IRE
Cataractes bilaterals
Hierro ferritina-L
Síndrome de catarata de hiperferritinemia hereditaria
Ferritina sérica
Metabolismo del hierro
Cataratas bilaterales
Ferro ferritin-L
Hereditary hyperferritinemia cataract syndrome
Serum ferritin
Iron metabolism
IRP / IRE regulatory system
Bilateral cataracts
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Descripción
Sumario:This work was supported by the grant PS09/00341 from “Instituto de Salud Carlos III”, Spanish Health Program, grant SAF2012-40106 from Ministry of Economy and Competitiveness (MINECO) and grant CIVP16A1857 “Ayudas a proyectos de Investigación en Ciéncias de la Vida Fundación Ramón Areces” to M.S. M.S. held a research contract under the Ramón y Cajal program from the Spanish Ministry of Science and Innovation (RYC-2008-02352). J.A. held a technician support contract under the “Contratos de Técnicos de apoyo a la investigación en el SNS” program from the “Instituto de Salud Carlos III”, Spanish Health Program (CA10/01114). M.U.M. acknowledges funding from the E-RARE/BMBF project 01GM1005 and the Dietmar Hopp Stiftung as well as support from the Center For Rare Diseases, Medical Center University of Heidelberg.