Deciphering the role of RBM10 in development and cancer using a genetic mouse model

Short explanation English To reveal how RBM10 loss contributes to development and cancer we have established Rbm10 constitutive and conditional knockout mouse models and have analyzed phenotypes at the organismal and cellular level. Constitutive inactivation of Rbm10 in the mouse germline results in...

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Detalles Bibliográficos
Autor: Maldonado Barragán, Ana Margarita
Tipo de recurso: tesis doctoral
Estado:Versión publicada
Fecha de publicación:2021
País:España
Institución:CBUC, CESCA
Repositorio:TDR. Tesis Doctorales en Red
OAI Identifier:oai:www.tdx.cat:10803/671367
Acceso en línea:http://hdl.handle.net/10803/671367
Access Level:acceso abierto
Palabra clave:RBM10 Alternative splicing Development Bladder cancer Organoids RBM10 Splicing alternativo Desarrollo Cáncer de Vejiga Organoides
RBM10
Alternative splicing
Development
Bladder cancer
Organoids
Splicing alternativo
Desarrollo
Cáncer de Vejiga
Organoides
616.6
Descripción
Sumario:Short explanation English To reveal how RBM10 loss contributes to development and cancer we have established Rbm10 constitutive and conditional knockout mouse models and have analyzed phenotypes at the organismal and cellular level. Constitutive inactivation of Rbm10 in the mouse germline results in partial male embryonic lethality and partially recapitulates TARP syndrome. Tissue-wide Rbm10 inactivation in young mice is well tolerated, indicating that the protein is dispensable in adulthood. In normal urothelial organoids, Rbm10 inactivation in vitro leads to partial EGF-independence and a luminal-like phenotype with stratified epithelium features. Further, our analysis on human tumors reveals that RBM10 inactivation is an early genetic alteration in bladder carcinogenesis. I have also generated several tools to further analyze the molecular mechanisms through which RBM10 loss-of-function contributes to bladder cancer. Altogether, the results validate the newly developed strain as a valuable model to study TARP syndrome and urothelial cancer, allowing the identification of RBM10-related splicing targets and molecular mechanisms relevant to disease progression