NCC: An R-package for analysis and simulation of platform trials with non-concurrent controls

Platform trials evaluate the efficacy of multiple treatments, allowing for late entry of the experimental arms and enabling efficiency gains by sharing controls. The power of individual treatment-control comparisons in such trials can be improved by utilizing non-concurrent controls (NCC) in the ana...

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Detalles Bibliográficos
Autores: Krotka, Pavla, Hees, Katharina, Jacko, Peter, Magirr, Dominic, Posch, Martin, Bofill Roig, Marta|||0000-0002-4400-7541
Tipo de recurso: artículo
Fecha de publicación:2023
País:España
Institución:Universitat Politècnica de Catalunya (UPC)
Repositorio:UPCommons. Portal del coneixement obert de la UPC
Idioma:inglés
OAI Identifier:oai:upcommons.upc.edu:2117/415926
Acceso en línea:https://hdl.handle.net/2117/415926
https://dx.doi.org/10.1016/j.softx.2023.101437
Access Level:acceso abierto
Palabra clave:Statistics
Clinical trial simulation
Platform trials
Shared controls
Non-concurrent controls
Àrees temàtiques de la UPC::Economia i organització d'empreses
Descripción
Sumario:Platform trials evaluate the efficacy of multiple treatments, allowing for late entry of the experimental arms and enabling efficiency gains by sharing controls. The power of individual treatment-control comparisons in such trials can be improved by utilizing non-concurrent controls (NCC) in the analysis. We present the R-package NCC for the design and analysis of platform trials using non-concurrent controls. NCC allows for simulating platform trials and evaluating the properties of analysis methods that make use of non-concurrent controls in a variety of settings. We describe the main NCC functions and show how to use the package to simulate and analyse platform trials by means of specific examples.