The ALS-Related o1R E102Q Mutant Eludes Ligand Control and Exhibits Anomalous Response to Calcium

Sigma receptor type 1 (o1R) is a transmembrane protein expressed throughout the central nervous system and in certain peripheral tissues. The human o1R E102Q mutation causes juvenile amyotrophic lateral sclerosis (ALS), likely by inducing a series of alterations in calcium efflux from the endoplasmi...

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Bibliographic Details
Authors: Rodríguez-Muñoz, María, Cortés-Montero, Elsa, Sánchez-Blázquez, Pilar, Garzón-Niño, Javier
Format: article
Status:Published version
Publication Date:2020
Country:España
Institution:Consejo Superior de Investigaciones Científicas (CSIC)
Repository:DIGITAL.CSIC. Repositorio Institucional del CSIC
OAI Identifier:oai:digital.csic.es:10261/238822
Online Access:http://hdl.handle.net/10261/238822
Access Level:Open access
Keyword:sigma type receptor 1
juvenile amyotrophic lateral sclerosis
E102Q mutation
N-methyl-D-aspartate receptor
transient receptor potential calcium channels
binding immunoglobulin protein
Description
Summary:Sigma receptor type 1 (o1R) is a transmembrane protein expressed throughout the central nervous system and in certain peripheral tissues. The human o1R E102Q mutation causes juvenile amyotrophic lateral sclerosis (ALS), likely by inducing a series of alterations in calcium efflux from the endoplasmic reticulum (ER) to mitochondria that affects calcium homeostasis and cellular survival. Here, we report the influence of calcium on o1R E102Q associations with glutamate N-methyl-D-aspartate receptors (NMDARs), binding immunoglobulin protein (BiP), and transient receptor potential calcium channels A1, V1, and M8. The mutant protein inhibited the binding of calmodulin to these calcium channels and interacted less with BiP than wild-type o1R, thereby contributing to calcium homeostasis dysfunction. Mutant o1R, but not wild-type o1R, strongly bound to histidine triad nucleotide binding protein 1, which regulates neuromuscular synaptic organization and target selection through teneurin 1. While ligands regulated the association of o1R wild-type with NMDARs and BiP, they failed to modulate the interaction between these proteins and the o1R E102Q mutant. Thus, the o1R E102Q mutant exhibited an anomalous response to cytosolic calcium levels, altered affinity for target proteins, and a loss of response to regulatory ligands. We believe that these modifications may contribute to the onset of juvenile ALS.