Novel Tissue-Specific Multifunctionalized Nanotechnological Platform Encapsulating Riluzole Against Motor Neuron Diseases

Motor neuron diseases are neurological disorders characterized by progressive degeneration of upper and/or lower motor neurons. Amyotrophic Lateral Sclerosis (ALS) is the most common form of motor neuron diseases, where patients suffer progressive paralysis, muscle atrophy and finally death. Despite...

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Detalles Bibliográficos
Autores: Esteruelas, Gerard, Ettcheto, Miren, Haro Villar, Isabel, Herrando-Grabulosa, Mireia, Gaja-Capdevila, Núria, Gómara Elena, María José, Navarro, Xavier, Espina, Marta, Souto, Eliana B., Camins, Antoni, García, Maria Luisa, Sánchez-López, Elena
Tipo de recurso: artículo
Estado:Versión publicada
Fecha de publicación:2025
País:España
Institución:Consejo Superior de Investigaciones Científicas (CSIC)
Repositorio:DIGITAL.CSIC. Repositorio Institucional del CSIC
OAI Identifier:oai:digital.csic.es:10261/383486
Acceso en línea:http://hdl.handle.net/10261/383486
https://api.elsevier.com/content/abstract/scopus_id/85219619217
Access Level:acceso abierto
Palabra clave:Riluzole
PLGA-PEG
Drug delivery system
Motor neuron disease
Nanomedicine
pVEC
http://metadata.un.org/sdg/3
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Descripción
Sumario:Motor neuron diseases are neurological disorders characterized by progressive degeneration of upper and/or lower motor neurons. Amyotrophic Lateral Sclerosis (ALS) is the most common form of motor neuron diseases, where patients suffer progressive paralysis, muscle atrophy and finally death. Despite ALS severity, no treatment is safe and fully effective. In this area, Riluzole was the first drug approved and it constitutes the gold-standard for this pathology. However, to obtain suitable therapeutic efficacy, Riluzole requires high doses that are associated with severe adverse effects in other tissues. To attain Riluzole therapeutic efficacy avoiding other organs side-effects, new therapeutic strategies to enhance the delivery of Riluzole specifically to motor neurons constitute an unmet medical need. In this area, we have developed a novel multifunctional nanostructurated carrier to selectively deliver Riluzole to motor neurons.