Winner's Curse Correction and Variable Thresholding Improve Performance of Polygenic Risk Modeling Based on Genome-Wide Association Study Summary-Level Data

Recent heritability analyses have indicated that genome-wide association studies (GWAS) have the potential to improve genetic risk prediction for complex diseases based on polygenic risk score (PRS), a simple modelling technique that can be implemented using summary-level data from the discovery sam...

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Autores: Shi, Jianxin, Park, Ju-Hyun, Duan, Jubao, Berndt, Sonja T, Moy, Winton, Yu, Kai, Song, Lei, Wheeler, William, Hua, Xing, Silverman, Debra, Garcia-Closas, Montserrat, Hsiung, Chao Agnes, Figueroa, Jonine D, Cortessis, Victoria K, Malats, Nuria, Karagas, Margaret R, Vineis, Paolo, Chang, I-Shou, Lin, Dongxin, Zhou, Baosen, Seow, Adeline, Matsuo, Keitaro, Hong, Yun-Chul, Caporaso, Neil E, Wolpin, Brian, Jacobs, Eric, Petersen, Gloria M, Klein, Alison P, Li, Donghui, Risch, Harvey, Sanders, Alan R, Hsu, Li, Schoen, Robert E, Brenner, Hermann, Stolzenberg-Solomon, Rachael, Gejman, Pablo, Lan, Qing, Rothman, Nathaniel, Amundadottir, Laufey T, Landi, Maria Teresa, Levinson, Douglas F, Chanock, Stephen J, Chatterjee, Nilanjan
Tipo de recurso: artículo
Fecha de publicación:2016
País:España
Institución:Instituto de Salud Carlos III (ISCIII)
Repositorio:Repisalud
Idioma:inglés
OAI Identifier:oai:repisalud.isciii.es:20.500.12105/7901
Acceso en línea:http://hdl.handle.net/20.500.12105/7901
Access Level:acceso abierto
Palabra clave:Algorithms
Computer Simulation
Genome-Wide Association Study
Humans
Linkage Disequilibrium
Multifactorial Inheritance
Polymorphism, Single Nucleotide
Risk Factors
Genetic Predisposition to Disease
Models, Genetic
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spelling Winner's Curse Correction and Variable Thresholding Improve Performance of Polygenic Risk Modeling Based on Genome-Wide Association Study Summary-Level DataShi, JianxinPark, Ju-HyunDuan, JubaoBerndt, Sonja TMoy, WintonYu, KaiSong, LeiWheeler, WilliamHua, XingSilverman, DebraGarcia-Closas, MontserratHsiung, Chao AgnesFigueroa, Jonine DCortessis, Victoria KMalats, NuriaKaragas, Margaret RVineis, PaoloChang, I-ShouLin, DongxinZhou, BaosenSeow, AdelineMatsuo, KeitaroHong, Yun-ChulCaporaso, Neil EWolpin, BrianJacobs, EricPetersen, Gloria MKlein, Alison PLi, DonghuiRisch, HarveySanders, Alan RHsu, LiSchoen, Robert EBrenner, HermannStolzenberg-Solomon, RachaelGejman, PabloLan, QingRothman, NathanielAmundadottir, Laufey TLandi, Maria TeresaLevinson, Douglas FChanock, Stephen JChatterjee, NilanjanAlgorithmsComputer SimulationGenome-Wide Association StudyHumansLinkage DisequilibriumMultifactorial InheritancePolymorphism, Single NucleotideRisk FactorsGenetic Predisposition to DiseaseModels, GeneticRecent heritability analyses have indicated that genome-wide association studies (GWAS) have the potential to improve genetic risk prediction for complex diseases based on polygenic risk score (PRS), a simple modelling technique that can be implemented using summary-level data from the discovery samples. We herein propose modifications to improve the performance of PRS. We introduce threshold-dependent winner's-curse adjustments for marginal association coefficients that are used to weight the single-nucleotide polymorphisms (SNPs) in PRS. Further, as a way to incorporate external functional/annotation knowledge that could identify subsets of SNPs highly enriched for associations, we propose variable thresholds for SNPs selection. We applied our methods to GWAS summary-level data of 14 complex diseases. Across all diseases, a simple winner's curse correction uniformly led to enhancement of performance of the models, whereas incorporation of functional SNPs was beneficial only for selected diseases. Compared to the standard PRS algorithm, the proposed methods in combination led to notable gain in efficiency (25-50% increase in the prediction R2) for 5 of 14 diseases. As an example, for GWAS of type 2 diabetes, winner's curse correction improved prediction R2 from 2.29% based on the standard PRS to 3.10% (P = 0.0017) and incorporating functional annotation data further improved R2 to 3.53% (P = 2×10-5). Our simulation studies illustrate why differential treatment of certain categories of functional SNPs, even when shown to be highly enriched for GWAS-heritability, does not lead to proportionate improvement in genetic risk-prediction because of non-uniform linkage disequilibrium structure.Public Library of Science (PLOS)NIH - National Cancer Institute (NCI) (Estados Unidos)Deutsche Forschungsgemeinschaft (Alemania)Federal Ministry of Education & Research (Alemania)NIH - National Heart, Lung, and Blood Institute (NHLBI) (Estados Unidos)20192019-07-1220162016-12-0120162016-12-01journal articlehttp://purl.org/coar/resource_type/c_6501VoRhttp://purl.org/coar/version/c_970fb48d4fbd8a85info:eu-repo/semantics/articleapplication/pdfhttp://hdl.handle.net/20.500.12105/7901reponame:Repisaludinstname:Instituto de Salud Carlos III (ISCIII)Inglésengopen accesshttp://purl.org/coar/access_right/c_abf2Atribución-NoComercial-CompartirIgual 4.0 Internacionalhttp://creativecommons.org/licenses/by-nc-sa/4.0/info:eu-repo/semantics/openAccessoai:repisalud.isciii.es:20.500.12105/79012026-06-12T12:43:37Z
dc.title.none.fl_str_mv Winner's Curse Correction and Variable Thresholding Improve Performance of Polygenic Risk Modeling Based on Genome-Wide Association Study Summary-Level Data
title Winner's Curse Correction and Variable Thresholding Improve Performance of Polygenic Risk Modeling Based on Genome-Wide Association Study Summary-Level Data
spellingShingle Winner's Curse Correction and Variable Thresholding Improve Performance of Polygenic Risk Modeling Based on Genome-Wide Association Study Summary-Level Data
Shi, Jianxin
Algorithms
Computer Simulation
Genome-Wide Association Study
Humans
Linkage Disequilibrium
Multifactorial Inheritance
Polymorphism, Single Nucleotide
Risk Factors
Genetic Predisposition to Disease
Models, Genetic
title_short Winner's Curse Correction and Variable Thresholding Improve Performance of Polygenic Risk Modeling Based on Genome-Wide Association Study Summary-Level Data
title_full Winner's Curse Correction and Variable Thresholding Improve Performance of Polygenic Risk Modeling Based on Genome-Wide Association Study Summary-Level Data
title_fullStr Winner's Curse Correction and Variable Thresholding Improve Performance of Polygenic Risk Modeling Based on Genome-Wide Association Study Summary-Level Data
title_full_unstemmed Winner's Curse Correction and Variable Thresholding Improve Performance of Polygenic Risk Modeling Based on Genome-Wide Association Study Summary-Level Data
title_sort Winner's Curse Correction and Variable Thresholding Improve Performance of Polygenic Risk Modeling Based on Genome-Wide Association Study Summary-Level Data
dc.creator.none.fl_str_mv Shi, Jianxin
Park, Ju-Hyun
Duan, Jubao
Berndt, Sonja T
Moy, Winton
Yu, Kai
Song, Lei
Wheeler, William
Hua, Xing
Silverman, Debra
Garcia-Closas, Montserrat
Hsiung, Chao Agnes
Figueroa, Jonine D
Cortessis, Victoria K
Malats, Nuria
Karagas, Margaret R
Vineis, Paolo
Chang, I-Shou
Lin, Dongxin
Zhou, Baosen
Seow, Adeline
Matsuo, Keitaro
Hong, Yun-Chul
Caporaso, Neil E
Wolpin, Brian
Jacobs, Eric
Petersen, Gloria M
Klein, Alison P
Li, Donghui
Risch, Harvey
Sanders, Alan R
Hsu, Li
Schoen, Robert E
Brenner, Hermann
Stolzenberg-Solomon, Rachael
Gejman, Pablo
Lan, Qing
Rothman, Nathaniel
Amundadottir, Laufey T
Landi, Maria Teresa
Levinson, Douglas F
Chanock, Stephen J
Chatterjee, Nilanjan
author Shi, Jianxin
author_facet Shi, Jianxin
Park, Ju-Hyun
Duan, Jubao
Berndt, Sonja T
Moy, Winton
Yu, Kai
Song, Lei
Wheeler, William
Hua, Xing
Silverman, Debra
Garcia-Closas, Montserrat
Hsiung, Chao Agnes
Figueroa, Jonine D
Cortessis, Victoria K
Malats, Nuria
Karagas, Margaret R
Vineis, Paolo
Chang, I-Shou
Lin, Dongxin
Zhou, Baosen
Seow, Adeline
Matsuo, Keitaro
Hong, Yun-Chul
Caporaso, Neil E
Wolpin, Brian
Jacobs, Eric
Petersen, Gloria M
Klein, Alison P
Li, Donghui
Risch, Harvey
Sanders, Alan R
Hsu, Li
Schoen, Robert E
Brenner, Hermann
Stolzenberg-Solomon, Rachael
Gejman, Pablo
Lan, Qing
Rothman, Nathaniel
Amundadottir, Laufey T
Landi, Maria Teresa
Levinson, Douglas F
Chanock, Stephen J
Chatterjee, Nilanjan
author_role author
author2 Park, Ju-Hyun
Duan, Jubao
Berndt, Sonja T
Moy, Winton
Yu, Kai
Song, Lei
Wheeler, William
Hua, Xing
Silverman, Debra
Garcia-Closas, Montserrat
Hsiung, Chao Agnes
Figueroa, Jonine D
Cortessis, Victoria K
Malats, Nuria
Karagas, Margaret R
Vineis, Paolo
Chang, I-Shou
Lin, Dongxin
Zhou, Baosen
Seow, Adeline
Matsuo, Keitaro
Hong, Yun-Chul
Caporaso, Neil E
Wolpin, Brian
Jacobs, Eric
Petersen, Gloria M
Klein, Alison P
Li, Donghui
Risch, Harvey
Sanders, Alan R
Hsu, Li
Schoen, Robert E
Brenner, Hermann
Stolzenberg-Solomon, Rachael
Gejman, Pablo
Lan, Qing
Rothman, Nathaniel
Amundadottir, Laufey T
Landi, Maria Teresa
Levinson, Douglas F
Chanock, Stephen J
Chatterjee, Nilanjan
author2_role author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
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author
author
author
author
dc.contributor.none.fl_str_mv NIH - National Cancer Institute (NCI) (Estados Unidos)
Deutsche Forschungsgemeinschaft (Alemania)
Federal Ministry of Education & Research (Alemania)
NIH - National Heart, Lung, and Blood Institute (NHLBI) (Estados Unidos)

dc.subject.none.fl_str_mv Algorithms
Computer Simulation
Genome-Wide Association Study
Humans
Linkage Disequilibrium
Multifactorial Inheritance
Polymorphism, Single Nucleotide
Risk Factors
Genetic Predisposition to Disease
Models, Genetic
topic Algorithms
Computer Simulation
Genome-Wide Association Study
Humans
Linkage Disequilibrium
Multifactorial Inheritance
Polymorphism, Single Nucleotide
Risk Factors
Genetic Predisposition to Disease
Models, Genetic
description Recent heritability analyses have indicated that genome-wide association studies (GWAS) have the potential to improve genetic risk prediction for complex diseases based on polygenic risk score (PRS), a simple modelling technique that can be implemented using summary-level data from the discovery samples. We herein propose modifications to improve the performance of PRS. We introduce threshold-dependent winner's-curse adjustments for marginal association coefficients that are used to weight the single-nucleotide polymorphisms (SNPs) in PRS. Further, as a way to incorporate external functional/annotation knowledge that could identify subsets of SNPs highly enriched for associations, we propose variable thresholds for SNPs selection. We applied our methods to GWAS summary-level data of 14 complex diseases. Across all diseases, a simple winner's curse correction uniformly led to enhancement of performance of the models, whereas incorporation of functional SNPs was beneficial only for selected diseases. Compared to the standard PRS algorithm, the proposed methods in combination led to notable gain in efficiency (25-50% increase in the prediction R2) for 5 of 14 diseases. As an example, for GWAS of type 2 diabetes, winner's curse correction improved prediction R2 from 2.29% based on the standard PRS to 3.10% (P = 0.0017) and incorporating functional annotation data further improved R2 to 3.53% (P = 2×10-5). Our simulation studies illustrate why differential treatment of certain categories of functional SNPs, even when shown to be highly enriched for GWAS-heritability, does not lead to proportionate improvement in genetic risk-prediction because of non-uniform linkage disequilibrium structure.
publishDate 2016
dc.date.none.fl_str_mv 2016
2016-12-01
2016
2016-12-01
2019
2019-07-12
dc.type.none.fl_str_mv journal article
http://purl.org/coar/resource_type/c_6501
VoR
http://purl.org/coar/version/c_970fb48d4fbd8a85
dc.type.openaire.fl_str_mv info:eu-repo/semantics/article
format article
dc.identifier.none.fl_str_mv http://hdl.handle.net/20.500.12105/7901
url http://hdl.handle.net/20.500.12105/7901
dc.language.none.fl_str_mv Inglés
eng
language_invalid_str_mv Inglés
language eng
dc.rights.none.fl_str_mv open access
http://purl.org/coar/access_right/c_abf2
Atribución-NoComercial-CompartirIgual 4.0 Internacional
http://creativecommons.org/licenses/by-nc-sa/4.0/
dc.rights.openaire.fl_str_mv info:eu-repo/semantics/openAccess
rights_invalid_str_mv open access
http://purl.org/coar/access_right/c_abf2
Atribución-NoComercial-CompartirIgual 4.0 Internacional
http://creativecommons.org/licenses/by-nc-sa/4.0/
eu_rights_str_mv openAccess
dc.format.none.fl_str_mv application/pdf
dc.publisher.none.fl_str_mv Public Library of Science (PLOS)
publisher.none.fl_str_mv Public Library of Science (PLOS)
dc.source.none.fl_str_mv reponame:Repisalud
instname:Instituto de Salud Carlos III (ISCIII)
instname_str Instituto de Salud Carlos III (ISCIII)
reponame_str Repisalud
collection Repisalud
repository.name.fl_str_mv
repository.mail.fl_str_mv
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