Oxetane Grafts Installed Site-Selectively on Native Disulfides to Enhance Protein Stability and Activity In Vivo

A four-membered oxygen ring (oxetane) can be readily grafted into native peptides and proteins through site-selective bis-alkylation of cysteine residues present as disulfides under mild and biocompatible conditions. The selective installation of the oxetane graft enhances stability and activity, as...

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Bibliographic Details
Authors: Martínez-Sáez, N. [0000-0002-0799-5106], Sun, S. [0000-0002-4384-7338], Oldrini, D., Sormanni, P., Boutureira, O. [0000-0002-0768-8309], Carboni, F., Compañón, I., Deery, M.J., Vendruscolo, M. [0000-0002-3616-1610], Corzana, F. [0000-0001-5597-8127], Adamo, R., Bernardes, G.J.L. [0000-0001-6594-8917]
Format: article
Status:Published version
Publication Date:2017
Country:España
Institution:Universidad de La Rioja (UR)
Repository:RIUR. Repositorio Institucional de la Universidad de La Rioja
OAI Identifier:oai:portal.dialnet.es:doc/5bbc68cbb750603269e80fb6
Online Access:https://investigacion.unirioja.es/documentos/5bbc68cbb750603269e80fb6
Access Level:Open access
Keyword:antibodies
disulfides
immunogenic proteins
oxetanes
stapling
Description
Summary:A four-membered oxygen ring (oxetane) can be readily grafted into native peptides and proteins through site-selective bis-alkylation of cysteine residues present as disulfides under mild and biocompatible conditions. The selective installation of the oxetane graft enhances stability and activity, as demonstrated for a range of biologically relevant cyclic peptides, including somatostatin, proteins, and antibodies, such as a Fab arm of the antibody Herceptin and a designed antibody DesAb-Aβ against the human Amyloid-β peptide. Oxetane grafting of the genetically detoxified diphtheria toxin CRM197 improves significantly the immunogenicity of this protein in mice, which illustrates the general utility of this strategy to modulate the stability and biological activity of therapeutic proteins containing disulfides in their structures. © 2017 The Authors. Published by Wiley-VCH Verlag GmbH & Co. KGaA.