Eculizumab as a promising treatment in thymoma-associated myasthenia gravis

Myasthenia gravis is a chronic autoimmune disorder caused by antibodies directed against the neuromuscular junction. Some patients may have an associated thymoma, which confers a worse prognosis. Eculizumab, a monoclonal antibody that inhibits the activation of terminal complement, has recently been...

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Detalhes bibliográficos
Autores: Vélez Santamaria, Valentina, Nedkova Hristova, Velina, Díez, Laura, Homedes, Christian, Alberti, Maria Antonia, Casasnovas Pons, Carlos
Tipo de documento: artigo
Estado:Versão publicada
Data de publicação:2020
País:España
Recursos:Varias* (Consorci de Biblioteques Universitáries de Catalunya, Centre de Serveis Científics i Acadèmics de Catalunya)
Repositório:Recercat. Dipósit de la Recerca de Catalunya
OAI Identifier:oai:recercat.cat:2445/171790
Acesso em linha:https://hdl.handle.net/2445/171790
Access Level:Acceso aberto
Palavra-chave:Malalties autoimmunitàries
Malalties neuromusculars
Autoimmune diseases
Neuromuscular diseases
Descrição
Resumo:Myasthenia gravis is a chronic autoimmune disorder caused by antibodies directed against the neuromuscular junction. Some patients may have an associated thymoma, which confers a worse prognosis. Eculizumab, a monoclonal antibody that inhibits the activation of terminal complement, has recently been approved for the treatment of refractory generalized myasthenia gravis. This is an early case report of thymoma-associated refractory myasthenia gravis successfully treated with eculizumab in a real-world setting.