Upregulation of NKG2D ligands impairs hematopoietic stem cell function in Fanconi anemia

Fanconi anemia (FA) is the most prevalent inherited bone marrow failure (BMF) syndrome. Nevertheless, the pathophysiological mechanisms of BMF in FA have not been fully elucidated. Since FA cells are defective in DNA repair, we hypothesized that FA hematopoietic stem and progenitor cells (HSPCs) mig...

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Detalles Bibliográficos
Autores: Casado, JA, Valeri, A, Sanchez-Dominguez, R, Vela, P, Lopez, A, Navarro, S, Alberquilla, O, Hanenberg, H, Pujol, R, Segovia, JC, Minguillon, J, Surralles, J, de Heredia, CD, Sevilla, J, Rio, P, Bueren, JA
Tipo de recurso: artículo
Estado:Versión publicada
Fecha de publicación:2022
País:España
Institución:Institut d’Investigació Biomèdica Sant Pau (IIB Sant Pau)
Repositorio:r-IIB SANT PAU. Repositorio Institucional de Producción Científica del Instituto de Investigación Biomédica Sant Pau
OAI Identifier:oai:iibsantpau.fundanetsuite.com:p12284
Acceso en línea:https://iibsantpau.fundanetsuite.com/Publicaciones/ProdCientif/PublicacionFrw.aspx?id=12284
https://ddd.uab.cat/record/277638
Access Level:acceso abierto
Palabra clave:ATM protein
ATR protein
CD135 antigen
CD16 antigen
CD3 antigen
CD34 antigen
CD4 antigen
CD56 antigen
CD69 antigen
CD8 antigen
chek 1 protein
Fanconi anemia group A protein
formaldehyde
hemoglobin
hemopoietic growth factor
mica protein
micb protein
mitomycin
natural killer cell receptor NKG2A
natural killer cell receptor NKG2D
protein inhibitor
sb 2118078
thrombopoietin
ulbp1 protein
ulbp2 protein
ulbp3 protein
ulbp4 protein
ulbp5 protein
ulbp6 protein
unclassified drug
ligand
natural killer cell lectin like receptor subfamily K
adolescent
adult
animal experiment
animal model
Article
bone marrow
CD8+ T lymphocyte
cell culture
cell function
child
clinical feature
controlled study
cytotoxicity
DNA damage
DNA repair
Fanconi anemia
female
fibroblast
genetic complementation
hematopoietic stem cell
human
human cell
immune system
in vivo study
innate immunity
male
mouse
nonhuman
preschool child
protein expression
prote
Descripción
Sumario:Fanconi anemia (FA) is the most prevalent inherited bone marrow failure (BMF) syndrome. Nevertheless, the pathophysiological mechanisms of BMF in FA have not been fully elucidated. Since FA cells are defective in DNA repair, we hypothesized that FA hematopoietic stem and progenitor cells (HSPCs) might express DNA damage-associated stress molecules such as natural killer group 2 member D ligands (NKG2D-Ls). These ligands could then interact with the activating NKG2D receptor expressed in cytotoxic NK or CD8(+) T cells, which may result in progressive HSPC depletion. Our results indeed demonstrated upregulated levels of NKG2D-Ls in cultured FA fibroblasts and T cells, and these levels were further exacerbated by mitomycin C or formaldehyde. Notably, a high proportion of BM CD34(+) HSPCs from patients with FA also expressed increased levels of NKG2D-Ls, which correlated inversely with the percentage of CD34(+) cells in BM. Remarkably, the reduced clonogenic potential characteristic of FA HSPCs was improved by blocking NKG2D-NKG2D-L interactions. Moreover, the in vivo blockage of these interactions in a BMF FA mouse model ameliorated the anemia in these animals. Our study demonstrates the involvement of NKG2D-NKG2D-L interactions in FA HSPC functionality, suggesting an unexpected role of the immune system in the progressive BMF that is characteristic of FA.