A multi-criteria decision analysis on the value of nintedanib for interstitial lung diseases

Objectives Our aim was to assess the value of nintedanib for non-idiopathic progressive fibrosing interstitial lung disease (non-IPF PF-ILD) and systemic sclerosis-associated ILD (SSc-ILD) in the Spanish context, using a multi-criteria decision analysis (MCDA). Methods Following an adaptation of the...

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Detalles Bibliográficos
Autores: Zozaya N., Arrizubieta Basterrechea M.I., Bollo E., Castellví I., Espín J., Ortego N., Poveda-Andrés J.L., Rodríguez Portal J.A., Rivero A., Marcos-Rodríguez J.A., Verde L.
Tipo de recurso: artículo
Estado:Versión publicada
Fecha de publicación:2022
País:España
Institución:Institut d’Investigació Biomèdica Sant Pau (IIB Sant Pau)
Repositorio:r-IIB SANT PAU. Repositorio Institucional de Producción Científica del Instituto de Investigación Biomédica Sant Pau
OAI Identifier:oai:iibsantpau.fundanetsuite.com:p15796
Acceso en línea:https://iibsantpau.fundanetsuite.com/Publicaciones/ProdCientif/PublicacionFrw.aspx?id=15796
Access Level:acceso abierto
Palabra clave:Biological organs
Patient treatment
Pulmonary diseases
Decision makers
Decisions makings
Interstitial lung disease
Linear modeling
Multi-criteria decision analysis
Positive value
Pulmonary fibrosis
Reproducibilities
Systemic sclerose
Weighting methods
Decision making
nintedanib
placebo
indole derivative
Article
clinician
controlled study
disease severity
drug efficacy
drug safety
drug tolerability
health care cost
human
interstitial lung disease
multicriteria decision analysis
non idiopathic progressive fibrosing interstitial lung disease
patient
patient-reported outcome
pharmacist
practice guideline
reproducibility
Spain
systemic sclerosis associated interstitial lung disease
treatment indication
unmet medical need
decision support system
disease exacerbation
Decision Support Techniques
Disease Progression
Humans
Descripción
Sumario:Objectives Our aim was to assess the value of nintedanib for non-idiopathic progressive fibrosing interstitial lung disease (non-IPF PF-ILD) and systemic sclerosis-associated ILD (SSc-ILD) in the Spanish context, using a multi-criteria decision analysis (MCDA). Methods Following an adaptation of the Evidence and Value: Impact on DEcision Making (EVIDEM) MCDA methodology, the estimated value of nintedanib was obtained by means of an additive linear model that combined individual weights (100-points distribution) of criteria with the individual scoring of nintedanib in each criterion for every indication, assigned by a multidisciplinary committee of twelve clinicians, patients, pharmacists, and decision-makers. To assess the reproducibility, an alternative weighting method was applied, as well as a re-test of weights and scores at a different moment of time. Results The experts committee recognized nintedanib as an intervention with a positive value contribution in comparison to placebo for the treatment of non-IPF PF-ILD (0.50 ± 0.16, on a scale from -1 to 1) and SSc-ILD (0.40 ± 0.12), diseases which were considered as very severe and with high unmet needs. The drug was perceived as a treatment that provides an added therapeutic benefit for patients (0.06-0.07), given its proven clinical efficacy (0.05-0.06), slight improvements in patient-reported outcomes (0.01-0.02), and similar safety profile than placebo (-0.04-0.00), which will likely be positioned as a recommended therapy in the next clinical practice guidelines updates. Conclusions Under this increasingly used methodology, nintedanib has shown to provide a positive value estimate for non-IPF PF-ILD and SSc-ILD when compared to placebo in Spain. © Author(s).