Identification of Lynch syndrome among patients with colorectal cancer

CONTEXT: Lynch syndrome is the most common form of hereditary colorectal cancer (CRC) and is caused by germline mutations in DNA mismatch repair (MMR) genes. Identification of gene carriers currently relies on germline analysis in patients with MMR-deficient tumors, but criteria to select individual...

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Autores: Moreira Ruiz, Leticia, Balaguer Prunés, Francesc, Lindor, Noralane, De la Chapelle, Albert, Hampel, Heather, Aaltonen, Lauri A., Hopper, John L., Le Marchand, Loic, Gallinger, Steven, Newcomb, Polly A., Haile, Robert, Thibodeau, Stephen N, Gunawardena, Shanaka, Jenkins, Mark A., Buchanan, Daniel D., Potter, John D., Baron, John A., Ahnen, Dennis J., Moreno Aguado, Víctor, Andreu, Montserrat, Ponz de Leon, Maurizio, Rustgi, Anil K., Castells Garangou, Antoni, EPICOLON Consortium
Formato: artículo
Estado:Versión publicada
Fecha de publicación:2012
País:España
Recursos:Varias* (Consorci de Biblioteques Universitáries de Catalunya, Centre de Serveis Científics i Acadèmics de Catalunya)
Repositorio:Recercat. Dipósit de la Recerca de Catalunya
OAI Identifier:oai:recercat.cat:2445/68389
Acesso em linha:https://hdl.handle.net/2445/68389
Access Level:acceso abierto
Palavra-chave:Càncer colorectal
Genètica molecular
Malalties hereditàries
Anàlisi multivariable
Colorectal cancer
Molecular genetics
Genetic diseases
Multivariate analysis
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spelling Identification of Lynch syndrome among patients with colorectal cancerMoreira Ruiz, LeticiaBalaguer Prunés, FrancescLindor, NoralaneDe la Chapelle, AlbertHampel, HeatherAaltonen, Lauri A.Hopper, John L.Le Marchand, LoicGallinger, StevenNewcomb, Polly A.Haile, RobertThibodeau, Stephen NGunawardena, ShanakaJenkins, Mark A.Buchanan, Daniel D.Potter, John D.Baron, John A.Ahnen, Dennis J.Moreno Aguado, VíctorAndreu, MontserratPonz de Leon, MaurizioRustgi, Anil K.Castells Garangou, AntoniEPICOLON ConsortiumCàncer colorectalGenètica molecularMalalties hereditàriesAnàlisi multivariableColorectal cancerMolecular geneticsGenetic diseasesMultivariate analysisCONTEXT: Lynch syndrome is the most common form of hereditary colorectal cancer (CRC) and is caused by germline mutations in DNA mismatch repair (MMR) genes. Identification of gene carriers currently relies on germline analysis in patients with MMR-deficient tumors, but criteria to select individuals in whom tumor MMR testing should be performed are unclear. OBJECTIVE: To establish a highly sensitive and efficient strategy for the identification of MMR gene mutation carriers among CRC probands. DESIGN, SETTING, AND PATIENTS: Pooled-data analysis of 4 large cohorts of newly diagnosed CRC probands recruited between 1994 and 2010 (n = 10,206) from the Colon Cancer Family Registry, the EPICOLON project, the Ohio State University, and the University of Helsinki examining personal, tumor-related, and family characteristics, as well as microsatellite instability, tumor MMR immunostaining, and germline MMR mutational status data. MAIN OUTCOME: Performance characteristics of selected strategies (Bethesda guidelines, Jerusalem recommendations, and those derived from a bivariate/multivariate analysis of variables associated with Lynch syndrome) were compared with tumor MMR testing of all CRC patients (universal screening). RESULTS: Of 10,206 informative, unrelated CRC probands, 312 (3.1%) were MMR gene mutation carriers. In the population-based cohorts (n = 3671 probands), the universal screening approach (sensitivity, 100%; 95% CI, 99.3%-100%; specificity, 93.0%; 95% CI, 92.0%-93.7%; diagnostic yield, 2.2%; 95% CI, 1.7%-2.7%) was superior to the use of Bethesda guidelines (sensitivity, 87.8%; 95% CI, 78.9%-93.2%; specificity, 97.5%; 95% CI, 96.9%-98.0%; diagnostic yield, 2.0%; 95% CI, 1.5%-2.4%; P < .001), Jerusalem recommendations (sensitivity, 85.4%; 95% CI, 77.1%-93.6%; specificity, 96.7%; 95% CI, 96.0%-97.2%; diagnostic yield, 1.9%; 95% CI, 1.4%-2.3%; P < .001), and a selective strategy based on tumor MMR testing of cases with CRC diagnosed at age 70 years or younger and in older patients fulfilling the Bethesda guidelines (sensitivity, 95.1%; 95% CI, 89.8%-99.0%; specificity, 95.5%; 95% CI, 94.7%-96.1%; diagnostic yield, 2.1%; 95% CI, 1.6%-2.6%; P < .001). This selective strategy missed 4.9% of Lynch syndrome cases but resulted in 34.8% fewer cases requiring tumor MMR testing and 28.6% fewer cases undergoing germline mutational analysis than the universal approach. CONCLUSION: Universal tumor MMR testing among CRC probands had a greater sensitivity for the identification of Lynch syndrome compared with multiple alternative strategies, although the increase in the diagnostic yield was modest.American Medical Association2015201520122015info:eu-repo/semantics/articleinfo:eu-repo/semantics/publishedVersion11 p.application/pdfhttps://hdl.handle.net/2445/68389Articles publicats en revistes (Ciències Clíniques)reponame:Recercat. Dipósit de la Recerca de Catalunyainstname:Varias* (Consorci de Biblioteques Universitáries de Catalunya, Centre de Serveis Científics i Acadèmics de Catalunya)InglésReproducció del document publicat a: http://dx.doi.org/10.1001/jama.2012.13088JAMA-Journal of the American Medical Association, 2012, vol. 308, num. 15, p. 1555-1565http://dx.doi.org/10.1001/jama.2012.13088info:eu-repo/grantAgreement/EC/FP7/268648(c) American Medical Association, 2012info:eu-repo/semantics/openAccessoai:recercat.cat:2445/683892026-05-29T05:05:01Z
dc.title.none.fl_str_mv Identification of Lynch syndrome among patients with colorectal cancer
title Identification of Lynch syndrome among patients with colorectal cancer
spellingShingle Identification of Lynch syndrome among patients with colorectal cancer
Moreira Ruiz, Leticia
Càncer colorectal
Genètica molecular
Malalties hereditàries
Anàlisi multivariable
Colorectal cancer
Molecular genetics
Genetic diseases
Multivariate analysis
title_short Identification of Lynch syndrome among patients with colorectal cancer
title_full Identification of Lynch syndrome among patients with colorectal cancer
title_fullStr Identification of Lynch syndrome among patients with colorectal cancer
title_full_unstemmed Identification of Lynch syndrome among patients with colorectal cancer
title_sort Identification of Lynch syndrome among patients with colorectal cancer
dc.creator.none.fl_str_mv Moreira Ruiz, Leticia
Balaguer Prunés, Francesc
Lindor, Noralane
De la Chapelle, Albert
Hampel, Heather
Aaltonen, Lauri A.
Hopper, John L.
Le Marchand, Loic
Gallinger, Steven
Newcomb, Polly A.
Haile, Robert
Thibodeau, Stephen N
Gunawardena, Shanaka
Jenkins, Mark A.
Buchanan, Daniel D.
Potter, John D.
Baron, John A.
Ahnen, Dennis J.
Moreno Aguado, Víctor
Andreu, Montserrat
Ponz de Leon, Maurizio
Rustgi, Anil K.
Castells Garangou, Antoni
EPICOLON Consortium
author Moreira Ruiz, Leticia
author_facet Moreira Ruiz, Leticia
Balaguer Prunés, Francesc
Lindor, Noralane
De la Chapelle, Albert
Hampel, Heather
Aaltonen, Lauri A.
Hopper, John L.
Le Marchand, Loic
Gallinger, Steven
Newcomb, Polly A.
Haile, Robert
Thibodeau, Stephen N
Gunawardena, Shanaka
Jenkins, Mark A.
Buchanan, Daniel D.
Potter, John D.
Baron, John A.
Ahnen, Dennis J.
Moreno Aguado, Víctor
Andreu, Montserrat
Ponz de Leon, Maurizio
Rustgi, Anil K.
Castells Garangou, Antoni
EPICOLON Consortium
author_role author
author2 Balaguer Prunés, Francesc
Lindor, Noralane
De la Chapelle, Albert
Hampel, Heather
Aaltonen, Lauri A.
Hopper, John L.
Le Marchand, Loic
Gallinger, Steven
Newcomb, Polly A.
Haile, Robert
Thibodeau, Stephen N
Gunawardena, Shanaka
Jenkins, Mark A.
Buchanan, Daniel D.
Potter, John D.
Baron, John A.
Ahnen, Dennis J.
Moreno Aguado, Víctor
Andreu, Montserrat
Ponz de Leon, Maurizio
Rustgi, Anil K.
Castells Garangou, Antoni
EPICOLON Consortium
author2_role author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
dc.subject.none.fl_str_mv Càncer colorectal
Genètica molecular
Malalties hereditàries
Anàlisi multivariable
Colorectal cancer
Molecular genetics
Genetic diseases
Multivariate analysis
topic Càncer colorectal
Genètica molecular
Malalties hereditàries
Anàlisi multivariable
Colorectal cancer
Molecular genetics
Genetic diseases
Multivariate analysis
description CONTEXT: Lynch syndrome is the most common form of hereditary colorectal cancer (CRC) and is caused by germline mutations in DNA mismatch repair (MMR) genes. Identification of gene carriers currently relies on germline analysis in patients with MMR-deficient tumors, but criteria to select individuals in whom tumor MMR testing should be performed are unclear. OBJECTIVE: To establish a highly sensitive and efficient strategy for the identification of MMR gene mutation carriers among CRC probands. DESIGN, SETTING, AND PATIENTS: Pooled-data analysis of 4 large cohorts of newly diagnosed CRC probands recruited between 1994 and 2010 (n = 10,206) from the Colon Cancer Family Registry, the EPICOLON project, the Ohio State University, and the University of Helsinki examining personal, tumor-related, and family characteristics, as well as microsatellite instability, tumor MMR immunostaining, and germline MMR mutational status data. MAIN OUTCOME: Performance characteristics of selected strategies (Bethesda guidelines, Jerusalem recommendations, and those derived from a bivariate/multivariate analysis of variables associated with Lynch syndrome) were compared with tumor MMR testing of all CRC patients (universal screening). RESULTS: Of 10,206 informative, unrelated CRC probands, 312 (3.1%) were MMR gene mutation carriers. In the population-based cohorts (n = 3671 probands), the universal screening approach (sensitivity, 100%; 95% CI, 99.3%-100%; specificity, 93.0%; 95% CI, 92.0%-93.7%; diagnostic yield, 2.2%; 95% CI, 1.7%-2.7%) was superior to the use of Bethesda guidelines (sensitivity, 87.8%; 95% CI, 78.9%-93.2%; specificity, 97.5%; 95% CI, 96.9%-98.0%; diagnostic yield, 2.0%; 95% CI, 1.5%-2.4%; P < .001), Jerusalem recommendations (sensitivity, 85.4%; 95% CI, 77.1%-93.6%; specificity, 96.7%; 95% CI, 96.0%-97.2%; diagnostic yield, 1.9%; 95% CI, 1.4%-2.3%; P < .001), and a selective strategy based on tumor MMR testing of cases with CRC diagnosed at age 70 years or younger and in older patients fulfilling the Bethesda guidelines (sensitivity, 95.1%; 95% CI, 89.8%-99.0%; specificity, 95.5%; 95% CI, 94.7%-96.1%; diagnostic yield, 2.1%; 95% CI, 1.6%-2.6%; P < .001). This selective strategy missed 4.9% of Lynch syndrome cases but resulted in 34.8% fewer cases requiring tumor MMR testing and 28.6% fewer cases undergoing germline mutational analysis than the universal approach. CONCLUSION: Universal tumor MMR testing among CRC probands had a greater sensitivity for the identification of Lynch syndrome compared with multiple alternative strategies, although the increase in the diagnostic yield was modest.
publishDate 2012
dc.date.none.fl_str_mv 2012
2015
2015
2015
dc.type.none.fl_str_mv info:eu-repo/semantics/article
info:eu-repo/semantics/publishedVersion
format article
status_str publishedVersion
dc.identifier.none.fl_str_mv https://hdl.handle.net/2445/68389
url https://hdl.handle.net/2445/68389
dc.language.none.fl_str_mv Inglés
language_invalid_str_mv Inglés
dc.relation.none.fl_str_mv Reproducció del document publicat a: http://dx.doi.org/10.1001/jama.2012.13088
JAMA-Journal of the American Medical Association, 2012, vol. 308, num. 15, p. 1555-1565
http://dx.doi.org/10.1001/jama.2012.13088
info:eu-repo/grantAgreement/EC/FP7/268648
dc.rights.none.fl_str_mv (c) American Medical Association, 2012
info:eu-repo/semantics/openAccess
rights_invalid_str_mv (c) American Medical Association, 2012
eu_rights_str_mv openAccess
dc.format.none.fl_str_mv 11 p.
application/pdf
dc.publisher.none.fl_str_mv American Medical Association
publisher.none.fl_str_mv American Medical Association
dc.source.none.fl_str_mv Articles publicats en revistes (Ciències Clíniques)
reponame:Recercat. Dipósit de la Recerca de Catalunya
instname:Varias* (Consorci de Biblioteques Universitáries de Catalunya, Centre de Serveis Científics i Acadèmics de Catalunya)
instname_str Varias* (Consorci de Biblioteques Universitáries de Catalunya, Centre de Serveis Científics i Acadèmics de Catalunya)
reponame_str Recercat. Dipósit de la Recerca de Catalunya
collection Recercat. Dipósit de la Recerca de Catalunya
repository.name.fl_str_mv
repository.mail.fl_str_mv
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