Adenovirus-mediated inducible expression of a PD-L1 blocking antibody in combination with macrophage depletion improves survival in a mouse model of peritoneal carcinomatosis

Immune checkpoint inhibitors (ICIs) have demonstrated remarkable efficacy in a growing number of malignancies. However, overcoming primary or secondary resistances is difficult due to pharmacokinetics issues and side effects associated with high systemic exposure. Local or regional expression of mon...

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Autores: Buñuales, M. (María)|||/items/80f24424-99e3-421f-9398-c067c56bf099, Ballesteros-Briones, M.C. (María Cristina)|||/items/4ede3e7d-1b82-4945-a24c-a96d8e2dff71, Gonzalez-Aparicio, M. (Manuela)|||/items/5d489890-239c-4227-8485-16049b53502e, Hervas-Stubbs, S. (Sandra)|||/items/8f56cb52-4465-4428-8acf-e50439c6be8f, Eva Martisova |||/items/80cb8569-6236-4f78-b528-c3d5bfc8efde, Mancheño, U. (Uxua)|||/items/7e9b5aee-3e45-40fb-b87f-19be6c19dd6c, Ricobaraza, A. (Ana)|||/items/a537e067-03df-4041-b520-0d8a5bd924ab, Lumbreras, S. (Sara)|||/items/a25d12b6-a452-41b1-835b-ccc8b653c31c, Smerdou-Picazo, C. (Cristian)|||/items/48fd1bd4-6483-45c9-9951-8a1b04873227, Hernández-Alcoceba, R. (Rubén)|||/items/c10dc855-ee3e-41a7-a4cf-2783e1a36f5e
Tipo de documento: artigo
Data de publicação:2021
País:España
Recursos:Universidad de Navarra
Repositório:Dadun. Depósito Académico Digital de la Universidad de Navarra
Idioma:inglês
OAI Identifier:oai:dadun.unav.edu:10171/115134
Acesso em linha:https://hdl.handle.net/10171/115134
Access Level:Acceso aberto
Palavra-chave:PD-L1
Adenovirus
Clodronate
Colorectal cancer
Drug-inducible system
High-capacity adenoviral vector
Immune checkpoint inhibitor
Macrophages
Mifepristone
Peritoneal carcinomatosis
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spelling Adenovirus-mediated inducible expression of a PD-L1 blocking antibody in combination with macrophage depletion improves survival in a mouse model of peritoneal carcinomatosisBuñuales, M. (María)|||/items/80f24424-99e3-421f-9398-c067c56bf099Ballesteros-Briones, M.C. (María Cristina)|||/items/4ede3e7d-1b82-4945-a24c-a96d8e2dff71Gonzalez-Aparicio, M. (Manuela)|||/items/5d489890-239c-4227-8485-16049b53502eHervas-Stubbs, S. (Sandra)|||/items/8f56cb52-4465-4428-8acf-e50439c6be8fEva Martisova |||/items/80cb8569-6236-4f78-b528-c3d5bfc8efdeMancheño, U. (Uxua)|||/items/7e9b5aee-3e45-40fb-b87f-19be6c19dd6cRicobaraza, A. (Ana)|||/items/a537e067-03df-4041-b520-0d8a5bd924abLumbreras, S. (Sara)|||/items/a25d12b6-a452-41b1-835b-ccc8b653c31cSmerdou-Picazo, C. (Cristian)|||/items/48fd1bd4-6483-45c9-9951-8a1b04873227Hernández-Alcoceba, R. (Rubén)|||/items/c10dc855-ee3e-41a7-a4cf-2783e1a36f5ePD-L1AdenovirusClodronateColorectal cancerDrug-inducible systemHigh-capacity adenoviral vectorImmune checkpoint inhibitorMacrophagesMifepristonePeritoneal carcinomatosisImmune checkpoint inhibitors (ICIs) have demonstrated remarkable efficacy in a growing number of malignancies. However, overcoming primary or secondary resistances is difficult due to pharmacokinetics issues and side effects associated with high systemic exposure. Local or regional expression of monoclonal antibodies (mAbs) using gene therapy vectors can alleviate this problem. In this work, we describe a high-capacity adenoviral vector (HCA-EFZP-aPDL1) equipped with a mifepristone-inducible system for the controlled expression of an anti-programmed death ligand 1 (PD-L1) blocking antibody. The vector was tested in an immune-competent mouse model of colorectal cancer based on implantation of MC38 cells. A single local administration of HCA-EFZP-aPDL1 in subcutaneous lesions led to a significant reduction in tumor growth with minimal release of the antibody in the circulation. When the vector was tested in a more stringent setting (rapidly progressing peritoneal carcinomatosis), the antitumor effect was marginal even in combination with other immune-stimulatory agents such as polyinosinic-polycytidylic acid (pI:C), blocking mAbs for T cell immunoglobulin, mucin-domain containing-3 (TIM-3) or agonistic mAbs for 4-1BB (CD137). In contrast, macrophage depletion by clodronate liposomes enhanced the efficacy of HCA-EFZP-aPDL1. These results highlight the importance of addressing macrophage-associated immunoregulatory mechanisms to overcome resistance to ICIs in the context of colorectal cancer.MDPIDadun. Depósito Académico Digital Universidad de Navarra20212021-01-0120212021-01-01journal articlehttp://purl.org/coar/resource_type/c_6501info:eu-repo/semantics/articleapplication/pdfhttps://hdl.handle.net/10171/115134reponame:Dadun. Depósito Académico Digital de la Universidad de Navarrainstname:Universidad de NavarraInglésengopen accesshttp://purl.org/coar/access_right/c_abf2info:eu-repo/semantics/openAccessoai:dadun.unav.edu:10171/1151342026-06-21T12:47:57Z
dc.title.none.fl_str_mv Adenovirus-mediated inducible expression of a PD-L1 blocking antibody in combination with macrophage depletion improves survival in a mouse model of peritoneal carcinomatosis
title Adenovirus-mediated inducible expression of a PD-L1 blocking antibody in combination with macrophage depletion improves survival in a mouse model of peritoneal carcinomatosis
spellingShingle Adenovirus-mediated inducible expression of a PD-L1 blocking antibody in combination with macrophage depletion improves survival in a mouse model of peritoneal carcinomatosis
Buñuales, M. (María)|||/items/80f24424-99e3-421f-9398-c067c56bf099
PD-L1
Adenovirus
Clodronate
Colorectal cancer
Drug-inducible system
High-capacity adenoviral vector
Immune checkpoint inhibitor
Macrophages
Mifepristone
Peritoneal carcinomatosis
title_short Adenovirus-mediated inducible expression of a PD-L1 blocking antibody in combination with macrophage depletion improves survival in a mouse model of peritoneal carcinomatosis
title_full Adenovirus-mediated inducible expression of a PD-L1 blocking antibody in combination with macrophage depletion improves survival in a mouse model of peritoneal carcinomatosis
title_fullStr Adenovirus-mediated inducible expression of a PD-L1 blocking antibody in combination with macrophage depletion improves survival in a mouse model of peritoneal carcinomatosis
title_full_unstemmed Adenovirus-mediated inducible expression of a PD-L1 blocking antibody in combination with macrophage depletion improves survival in a mouse model of peritoneal carcinomatosis
title_sort Adenovirus-mediated inducible expression of a PD-L1 blocking antibody in combination with macrophage depletion improves survival in a mouse model of peritoneal carcinomatosis
dc.creator.none.fl_str_mv Buñuales, M. (María)|||/items/80f24424-99e3-421f-9398-c067c56bf099
Ballesteros-Briones, M.C. (María Cristina)|||/items/4ede3e7d-1b82-4945-a24c-a96d8e2dff71
Gonzalez-Aparicio, M. (Manuela)|||/items/5d489890-239c-4227-8485-16049b53502e
Hervas-Stubbs, S. (Sandra)|||/items/8f56cb52-4465-4428-8acf-e50439c6be8f
Eva Martisova |||/items/80cb8569-6236-4f78-b528-c3d5bfc8efde
Mancheño, U. (Uxua)|||/items/7e9b5aee-3e45-40fb-b87f-19be6c19dd6c
Ricobaraza, A. (Ana)|||/items/a537e067-03df-4041-b520-0d8a5bd924ab
Lumbreras, S. (Sara)|||/items/a25d12b6-a452-41b1-835b-ccc8b653c31c
Smerdou-Picazo, C. (Cristian)|||/items/48fd1bd4-6483-45c9-9951-8a1b04873227
Hernández-Alcoceba, R. (Rubén)|||/items/c10dc855-ee3e-41a7-a4cf-2783e1a36f5e
author Buñuales, M. (María)|||/items/80f24424-99e3-421f-9398-c067c56bf099
author_facet Buñuales, M. (María)|||/items/80f24424-99e3-421f-9398-c067c56bf099
Ballesteros-Briones, M.C. (María Cristina)|||/items/4ede3e7d-1b82-4945-a24c-a96d8e2dff71
Gonzalez-Aparicio, M. (Manuela)|||/items/5d489890-239c-4227-8485-16049b53502e
Hervas-Stubbs, S. (Sandra)|||/items/8f56cb52-4465-4428-8acf-e50439c6be8f
Eva Martisova |||/items/80cb8569-6236-4f78-b528-c3d5bfc8efde
Mancheño, U. (Uxua)|||/items/7e9b5aee-3e45-40fb-b87f-19be6c19dd6c
Ricobaraza, A. (Ana)|||/items/a537e067-03df-4041-b520-0d8a5bd924ab
Lumbreras, S. (Sara)|||/items/a25d12b6-a452-41b1-835b-ccc8b653c31c
Smerdou-Picazo, C. (Cristian)|||/items/48fd1bd4-6483-45c9-9951-8a1b04873227
Hernández-Alcoceba, R. (Rubén)|||/items/c10dc855-ee3e-41a7-a4cf-2783e1a36f5e
author_role author
author2 Ballesteros-Briones, M.C. (María Cristina)|||/items/4ede3e7d-1b82-4945-a24c-a96d8e2dff71
Gonzalez-Aparicio, M. (Manuela)|||/items/5d489890-239c-4227-8485-16049b53502e
Hervas-Stubbs, S. (Sandra)|||/items/8f56cb52-4465-4428-8acf-e50439c6be8f
Eva Martisova |||/items/80cb8569-6236-4f78-b528-c3d5bfc8efde
Mancheño, U. (Uxua)|||/items/7e9b5aee-3e45-40fb-b87f-19be6c19dd6c
Ricobaraza, A. (Ana)|||/items/a537e067-03df-4041-b520-0d8a5bd924ab
Lumbreras, S. (Sara)|||/items/a25d12b6-a452-41b1-835b-ccc8b653c31c
Smerdou-Picazo, C. (Cristian)|||/items/48fd1bd4-6483-45c9-9951-8a1b04873227
Hernández-Alcoceba, R. (Rubén)|||/items/c10dc855-ee3e-41a7-a4cf-2783e1a36f5e
author2_role author
author
author
author
author
author
author
author
author
dc.contributor.none.fl_str_mv Dadun. Depósito Académico Digital Universidad de Navarra
dc.subject.none.fl_str_mv PD-L1
Adenovirus
Clodronate
Colorectal cancer
Drug-inducible system
High-capacity adenoviral vector
Immune checkpoint inhibitor
Macrophages
Mifepristone
Peritoneal carcinomatosis
topic PD-L1
Adenovirus
Clodronate
Colorectal cancer
Drug-inducible system
High-capacity adenoviral vector
Immune checkpoint inhibitor
Macrophages
Mifepristone
Peritoneal carcinomatosis
description Immune checkpoint inhibitors (ICIs) have demonstrated remarkable efficacy in a growing number of malignancies. However, overcoming primary or secondary resistances is difficult due to pharmacokinetics issues and side effects associated with high systemic exposure. Local or regional expression of monoclonal antibodies (mAbs) using gene therapy vectors can alleviate this problem. In this work, we describe a high-capacity adenoviral vector (HCA-EFZP-aPDL1) equipped with a mifepristone-inducible system for the controlled expression of an anti-programmed death ligand 1 (PD-L1) blocking antibody. The vector was tested in an immune-competent mouse model of colorectal cancer based on implantation of MC38 cells. A single local administration of HCA-EFZP-aPDL1 in subcutaneous lesions led to a significant reduction in tumor growth with minimal release of the antibody in the circulation. When the vector was tested in a more stringent setting (rapidly progressing peritoneal carcinomatosis), the antitumor effect was marginal even in combination with other immune-stimulatory agents such as polyinosinic-polycytidylic acid (pI:C), blocking mAbs for T cell immunoglobulin, mucin-domain containing-3 (TIM-3) or agonistic mAbs for 4-1BB (CD137). In contrast, macrophage depletion by clodronate liposomes enhanced the efficacy of HCA-EFZP-aPDL1. These results highlight the importance of addressing macrophage-associated immunoregulatory mechanisms to overcome resistance to ICIs in the context of colorectal cancer.
publishDate 2021
dc.date.none.fl_str_mv 2021
2021-01-01
2021
2021-01-01
dc.type.none.fl_str_mv journal article
http://purl.org/coar/resource_type/c_6501
dc.type.openaire.fl_str_mv info:eu-repo/semantics/article
format article
dc.identifier.none.fl_str_mv https://hdl.handle.net/10171/115134
url https://hdl.handle.net/10171/115134
dc.language.none.fl_str_mv Inglés
eng
language_invalid_str_mv Inglés
language eng
dc.rights.none.fl_str_mv open access
http://purl.org/coar/access_right/c_abf2
dc.rights.openaire.fl_str_mv info:eu-repo/semantics/openAccess
rights_invalid_str_mv open access
http://purl.org/coar/access_right/c_abf2
eu_rights_str_mv openAccess
dc.format.none.fl_str_mv application/pdf
dc.publisher.none.fl_str_mv MDPI
publisher.none.fl_str_mv MDPI
dc.source.none.fl_str_mv reponame:Dadun. Depósito Académico Digital de la Universidad de Navarra
instname:Universidad de Navarra
instname_str Universidad de Navarra
reponame_str Dadun. Depósito Académico Digital de la Universidad de Navarra
collection Dadun. Depósito Académico Digital de la Universidad de Navarra
repository.name.fl_str_mv
repository.mail.fl_str_mv
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