Adjuvant Pembrolizumab versus Placebo in Resected Stage III Melanoma

BACKGROUND The programmed death 1 (PD-1) inhibitor pembrolizumab has been found to prolong progression-free and overall survival among patients with advanced melanoma. We conducted a phase 3 double-blind trial to evaluate pembrolizumab as adjuvant therapy in patients with resected, high-risk stage I...

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Autores: Eggermont, Alexander Maximiliaan, Blank, C.U., Mandala, Mario, Long, Georgina V., Atkinson, Victoria, Dalle, Stéphane, Haydon, Andrew, Lichinitser, Mikhail, Khattak, Adnan, Carlino, Matteo S., Sandhu, Shahneen, Larkin, James, Puig i Sardà, Susana, Ascierto, Paolo Antonio, Rutkowski, Piotr, Schadendorf, Dirk, Koornstra, Rutger, Hernandez Aya, Leonel, Maio, Michele, Eertwegh, Alfonsus J.M. van den, Grob, Jean Jacques, Gutzmer, Ralf, Jamal, Rahima, Lorigan, Paul, Ibrahim, Nageatte, Marreaud, Sandrine, Akkooi, Alexander Christopher Jonathan van, Suciu, Stefan, Robert, Caroline
Tipo de recurso: artículo
Estado:Versión publicada
Fecha de publicación:2018
País:España
Institución:Universidad de Barcelona
Repositorio:Dipòsit Digital de la UB
OAI Identifier:oai:diposit.ub.edu:2445/132151
Acceso en línea:https://hdl.handle.net/2445/132151
Access Level:acceso abierto
Palabra clave:Melanoma
Placebos
Tractament adjuvant del càncer
Placebos (Medicine)
Adjuvant treatment of cancer
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spelling Adjuvant Pembrolizumab versus Placebo in Resected Stage III MelanomaEggermont, Alexander MaximiliaanBlank, C.U.Mandala, MarioLong, Georgina V.Atkinson, VictoriaDalle, StéphaneHaydon, AndrewLichinitser, MikhailKhattak, AdnanCarlino, Matteo S.Sandhu, ShahneenLarkin, JamesPuig i Sardà, SusanaAscierto, Paolo AntonioRutkowski, PiotrSchadendorf, DirkKoornstra, RutgerHernandez Aya, LeonelMaio, MicheleEertwegh, Alfonsus J.M. van denGrob, Jean JacquesGutzmer, RalfJamal, RahimaLorigan, PaulIbrahim, NageatteMarreaud, SandrineAkkooi, Alexander Christopher Jonathan vanSuciu, StefanRobert, CarolineMelanomaPlacebosTractament adjuvant del càncerMelanomaPlacebos (Medicine)Adjuvant treatment of cancerBACKGROUND The programmed death 1 (PD-1) inhibitor pembrolizumab has been found to prolong progression-free and overall survival among patients with advanced melanoma. We conducted a phase 3 double-blind trial to evaluate pembrolizumab as adjuvant therapy in patients with resected, high-risk stage III melanoma. METHODS Patients with completely resected stage III melanoma were randomly assigned (with stratification according to cancer stage and geographic region) to receive 200 mg of pembrolizumab (514 patients) or placebo (505 patients) intravenously every 3 weeks for a total of 18 doses (approximately 1 year) or until disease recurrence or unacceptable toxic effects occurred. Recurrence-free survival in the overall intention-to-treat population and in the subgroup of patients with cancer that was positive for the PD-1 ligand (PD-L1) were the primary end points. Safety was also evaluated. RESULTS At a median follow-up of 15 months, pembrolizumab was associated with significantly longer recurrence-free survival than placebo in the overall intention-to-treat population (1-year rate of recurrence-free survival, 75.4% [95% confidence interval {CI}, 71.3 to 78.9] vs. 61.0% [95% CI, 56.5 to 65.1]; hazard ratio for recurrence or death, 0.57; 98.4% CI, 0.43 to 0.74; P<0.001) and in the subgroup of 853 patients with PD-L1-positive tumors (1-year rate of recurrence-free survival, 77.1% [95% CI, 72.7 to 80.9] in the pembrolizumab group and 62.6% [95% CI, 57.7 to 67.0] in the placebo group; hazard ratio, 0.54; 95% CI, 0.42 to 0.69; P<0.001). Adverse events of grades 3 to 5 that were related to the trial regimen were reported in 14.7% of the patients in the pembrolizumab group and in 3.4% of patients in the placebo group. There was one treatment-related death due to myositis in the pembrolizumab group. CONCLUSIONS As adjuvant therapy for high-risk stage III melanoma, 200 mg of pembrolizumab administered every 3 weeks for up to 1 year resulted in significantly longer recurrencefree survival than placebo, with no new toxic effects identified. (Massachusetts Medical Society2018info:eu-repo/semantics/articleinfo:eu-repo/semantics/publishedVersionapplication/pdfhttps://hdl.handle.net/2445/132151Articles publicats en revistes (Medicina)reponame:Dipòsit Digital de la UBinstname:Universidad de BarcelonaInglésReproducció del document publicat a: https://doi.org/10.1056/NEJMoa1802357New England Journal of Medicine, 2018, vol. 378, num. 19, p. 1789-1801https://doi.org/10.1056/NEJMoa1802357(c) Massachusetts Medical Society, 2018info:eu-repo/semantics/openAccessoai:diposit.ub.edu:2445/1321512026-05-27T06:46:51Z
dc.title.none.fl_str_mv Adjuvant Pembrolizumab versus Placebo in Resected Stage III Melanoma
title Adjuvant Pembrolizumab versus Placebo in Resected Stage III Melanoma
spellingShingle Adjuvant Pembrolizumab versus Placebo in Resected Stage III Melanoma
Eggermont, Alexander Maximiliaan
Melanoma
Placebos
Tractament adjuvant del càncer
Melanoma
Placebos (Medicine)
Adjuvant treatment of cancer
title_short Adjuvant Pembrolizumab versus Placebo in Resected Stage III Melanoma
title_full Adjuvant Pembrolizumab versus Placebo in Resected Stage III Melanoma
title_fullStr Adjuvant Pembrolizumab versus Placebo in Resected Stage III Melanoma
title_full_unstemmed Adjuvant Pembrolizumab versus Placebo in Resected Stage III Melanoma
title_sort Adjuvant Pembrolizumab versus Placebo in Resected Stage III Melanoma
dc.creator.none.fl_str_mv Eggermont, Alexander Maximiliaan
Blank, C.U.
Mandala, Mario
Long, Georgina V.
Atkinson, Victoria
Dalle, Stéphane
Haydon, Andrew
Lichinitser, Mikhail
Khattak, Adnan
Carlino, Matteo S.
Sandhu, Shahneen
Larkin, James
Puig i Sardà, Susana
Ascierto, Paolo Antonio
Rutkowski, Piotr
Schadendorf, Dirk
Koornstra, Rutger
Hernandez Aya, Leonel
Maio, Michele
Eertwegh, Alfonsus J.M. van den
Grob, Jean Jacques
Gutzmer, Ralf
Jamal, Rahima
Lorigan, Paul
Ibrahim, Nageatte
Marreaud, Sandrine
Akkooi, Alexander Christopher Jonathan van
Suciu, Stefan
Robert, Caroline
author Eggermont, Alexander Maximiliaan
author_facet Eggermont, Alexander Maximiliaan
Blank, C.U.
Mandala, Mario
Long, Georgina V.
Atkinson, Victoria
Dalle, Stéphane
Haydon, Andrew
Lichinitser, Mikhail
Khattak, Adnan
Carlino, Matteo S.
Sandhu, Shahneen
Larkin, James
Puig i Sardà, Susana
Ascierto, Paolo Antonio
Rutkowski, Piotr
Schadendorf, Dirk
Koornstra, Rutger
Hernandez Aya, Leonel
Maio, Michele
Eertwegh, Alfonsus J.M. van den
Grob, Jean Jacques
Gutzmer, Ralf
Jamal, Rahima
Lorigan, Paul
Ibrahim, Nageatte
Marreaud, Sandrine
Akkooi, Alexander Christopher Jonathan van
Suciu, Stefan
Robert, Caroline
author_role author
author2 Blank, C.U.
Mandala, Mario
Long, Georgina V.
Atkinson, Victoria
Dalle, Stéphane
Haydon, Andrew
Lichinitser, Mikhail
Khattak, Adnan
Carlino, Matteo S.
Sandhu, Shahneen
Larkin, James
Puig i Sardà, Susana
Ascierto, Paolo Antonio
Rutkowski, Piotr
Schadendorf, Dirk
Koornstra, Rutger
Hernandez Aya, Leonel
Maio, Michele
Eertwegh, Alfonsus J.M. van den
Grob, Jean Jacques
Gutzmer, Ralf
Jamal, Rahima
Lorigan, Paul
Ibrahim, Nageatte
Marreaud, Sandrine
Akkooi, Alexander Christopher Jonathan van
Suciu, Stefan
Robert, Caroline
author2_role author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
dc.subject.none.fl_str_mv Melanoma
Placebos
Tractament adjuvant del càncer
Melanoma
Placebos (Medicine)
Adjuvant treatment of cancer
topic Melanoma
Placebos
Tractament adjuvant del càncer
Melanoma
Placebos (Medicine)
Adjuvant treatment of cancer
description BACKGROUND The programmed death 1 (PD-1) inhibitor pembrolizumab has been found to prolong progression-free and overall survival among patients with advanced melanoma. We conducted a phase 3 double-blind trial to evaluate pembrolizumab as adjuvant therapy in patients with resected, high-risk stage III melanoma. METHODS Patients with completely resected stage III melanoma were randomly assigned (with stratification according to cancer stage and geographic region) to receive 200 mg of pembrolizumab (514 patients) or placebo (505 patients) intravenously every 3 weeks for a total of 18 doses (approximately 1 year) or until disease recurrence or unacceptable toxic effects occurred. Recurrence-free survival in the overall intention-to-treat population and in the subgroup of patients with cancer that was positive for the PD-1 ligand (PD-L1) were the primary end points. Safety was also evaluated. RESULTS At a median follow-up of 15 months, pembrolizumab was associated with significantly longer recurrence-free survival than placebo in the overall intention-to-treat population (1-year rate of recurrence-free survival, 75.4% [95% confidence interval {CI}, 71.3 to 78.9] vs. 61.0% [95% CI, 56.5 to 65.1]; hazard ratio for recurrence or death, 0.57; 98.4% CI, 0.43 to 0.74; P<0.001) and in the subgroup of 853 patients with PD-L1-positive tumors (1-year rate of recurrence-free survival, 77.1% [95% CI, 72.7 to 80.9] in the pembrolizumab group and 62.6% [95% CI, 57.7 to 67.0] in the placebo group; hazard ratio, 0.54; 95% CI, 0.42 to 0.69; P<0.001). Adverse events of grades 3 to 5 that were related to the trial regimen were reported in 14.7% of the patients in the pembrolizumab group and in 3.4% of patients in the placebo group. There was one treatment-related death due to myositis in the pembrolizumab group. CONCLUSIONS As adjuvant therapy for high-risk stage III melanoma, 200 mg of pembrolizumab administered every 3 weeks for up to 1 year resulted in significantly longer recurrencefree survival than placebo, with no new toxic effects identified. (
publishDate 2018
dc.date.none.fl_str_mv 2018
dc.type.none.fl_str_mv info:eu-repo/semantics/article
info:eu-repo/semantics/publishedVersion
format article
status_str publishedVersion
dc.identifier.none.fl_str_mv https://hdl.handle.net/2445/132151
url https://hdl.handle.net/2445/132151
dc.language.none.fl_str_mv Inglés
language_invalid_str_mv Inglés
dc.relation.none.fl_str_mv Reproducció del document publicat a: https://doi.org/10.1056/NEJMoa1802357
New England Journal of Medicine, 2018, vol. 378, num. 19, p. 1789-1801
https://doi.org/10.1056/NEJMoa1802357
dc.rights.none.fl_str_mv (c) Massachusetts Medical Society, 2018
info:eu-repo/semantics/openAccess
rights_invalid_str_mv (c) Massachusetts Medical Society, 2018
eu_rights_str_mv openAccess
dc.format.none.fl_str_mv application/pdf
dc.publisher.none.fl_str_mv Massachusetts Medical Society
publisher.none.fl_str_mv Massachusetts Medical Society
dc.source.none.fl_str_mv Articles publicats en revistes (Medicina)
reponame:Dipòsit Digital de la UB
instname:Universidad de Barcelona
instname_str Universidad de Barcelona
reponame_str Dipòsit Digital de la UB
collection Dipòsit Digital de la UB
repository.name.fl_str_mv
repository.mail.fl_str_mv
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