Mitochondrial methylcytosines as blood-based biomarkers for Alzheimer's disease dementia prognosis

Alzheimer's Disease Dementia (ADD) prognosis is an unmet medical need. Mitochondrial dysfunction is an early AD etiopathogenic factor. The present study analyzed mitochondrial DNA (mtDNA) methylation patterns in blood samples from patients with mild cognitive impairment (MCI) who progressed to...

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Autores: Gascón-Bayarri, Jordi, Mosquera Mayo, José Luís, Blanch Lozano, Marta, Martí Benaiges, Pau, Fontal Aina, Beatriz, Trapero Candela, Carla, Rojo Fité, Nuria, Rico, Inma, Campdelacreu i Fumadó, Jaume, Fowler, Cristopher, Laws, Simon M., Tort Merino, Adrià, Sánchez del Valle Díaz, Raquel, Bello, Joan, Fortea Ormaechea, Juan, Lleó Bisa, Alberto, Mehanian, Courosh, Swerdlow, Russell H., Reñé Ramírez, Ramon, Barrachina, Marta
Tipo de recurso: artículo
Estado:Versión publicada
Fecha de publicación:2025
País:España
Institución:Universidad de Barcelona
Repositorio:Dipòsit Digital de la UB
OAI Identifier:oai:diposit.ub.edu:2445/224918
Acceso en línea:https://hdl.handle.net/2445/224918
Access Level:acceso abierto
Palabra clave:ADN mitocondrial
Malaltia d'Alzheimer
Neurociències
Metilació
Neurologia
Mitochondrial DNA
Alzheimer's disease
Neurosciences
Methylation
Neurology
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spelling Mitochondrial methylcytosines as blood-based biomarkers for Alzheimer's disease dementia prognosisGascón-Bayarri, JordiMosquera Mayo, José LuísBlanch Lozano, MartaMartí Benaiges, PauFontal Aina, BeatrizTrapero Candela, CarlaRojo Fité, NuriaRico, InmaCampdelacreu i Fumadó, JaumeFowler, CristopherLaws, Simon M.Tort Merino, AdriàSánchez del Valle Díaz, RaquelBello, JoanFortea Ormaechea, JuanLleó Bisa, AlbertoMehanian, CouroshSwerdlow, Russell H.Reñé Ramírez, RamonBarrachina, MartaADN mitocondrialMalaltia d'AlzheimerNeurociènciesMetilacióNeurologiaMitochondrial DNAAlzheimer's diseaseNeurosciencesMethylationNeurologyAlzheimer's Disease Dementia (ADD) prognosis is an unmet medical need. Mitochondrial dysfunction is an early AD etiopathogenic factor. The present study analyzed mitochondrial DNA (mtDNA) methylation patterns in blood samples from patients with mild cognitive impairment (MCI) who progressed to ADD (P), MCI remained stable (NP), and Cognitively Normal (CN) individuals. Differentially methylated sites were identified in the D-loop region in both CN vs. NP and NP vs. P comparisons, even before β-amyloid positivity. A Random Forest model was developed using mtDNA methylation data combined with cognitive and risk factor features. Model's performance was assessed by cross-validation and tested on an independent set, achieving 84.4% accuracy in training and 83.2% (95% CI: 75.2%-89.4%) in testing. For identifying P patients, sensitivity and specificity were 95.1% and 70.7%, respectively. The AUC-ROC was 90.3%. The developed model demonstrates predictive capacity in distinguishing cognitive decline and stability in MCI individuals, independently of their β-amyloid status.Elsevier2025info:eu-repo/semantics/articleinfo:eu-repo/semantics/publishedVersionapplication/pdfhttps://hdl.handle.net/2445/224918Articles publicats en revistes (Medicina)reponame:Dipòsit Digital de la UBinstname:Universidad de BarcelonaInglésReproducció del document publicat a: https://doi.org/10.1016/j.isci.2025.113418iScience, 2025, vol. 28, num. 9, 113418https://doi.org/10.1016/j.isci.2025.113418cc-by-nc-nd (c) Gascón-Bayarri, Jordi. et al., 2025http://creativecommons.org/licenses/by-nc-nd/4.0/info:eu-repo/semantics/openAccessoai:diposit.ub.edu:2445/2249182026-05-27T06:46:51Z
dc.title.none.fl_str_mv Mitochondrial methylcytosines as blood-based biomarkers for Alzheimer's disease dementia prognosis
title Mitochondrial methylcytosines as blood-based biomarkers for Alzheimer's disease dementia prognosis
spellingShingle Mitochondrial methylcytosines as blood-based biomarkers for Alzheimer's disease dementia prognosis
Gascón-Bayarri, Jordi
ADN mitocondrial
Malaltia d'Alzheimer
Neurociències
Metilació
Neurologia
Mitochondrial DNA
Alzheimer's disease
Neurosciences
Methylation
Neurology
title_short Mitochondrial methylcytosines as blood-based biomarkers for Alzheimer's disease dementia prognosis
title_full Mitochondrial methylcytosines as blood-based biomarkers for Alzheimer's disease dementia prognosis
title_fullStr Mitochondrial methylcytosines as blood-based biomarkers for Alzheimer's disease dementia prognosis
title_full_unstemmed Mitochondrial methylcytosines as blood-based biomarkers for Alzheimer's disease dementia prognosis
title_sort Mitochondrial methylcytosines as blood-based biomarkers for Alzheimer's disease dementia prognosis
dc.creator.none.fl_str_mv Gascón-Bayarri, Jordi
Mosquera Mayo, José Luís
Blanch Lozano, Marta
Martí Benaiges, Pau
Fontal Aina, Beatriz
Trapero Candela, Carla
Rojo Fité, Nuria
Rico, Inma
Campdelacreu i Fumadó, Jaume
Fowler, Cristopher
Laws, Simon M.
Tort Merino, Adrià
Sánchez del Valle Díaz, Raquel
Bello, Joan
Fortea Ormaechea, Juan
Lleó Bisa, Alberto
Mehanian, Courosh
Swerdlow, Russell H.
Reñé Ramírez, Ramon
Barrachina, Marta
author Gascón-Bayarri, Jordi
author_facet Gascón-Bayarri, Jordi
Mosquera Mayo, José Luís
Blanch Lozano, Marta
Martí Benaiges, Pau
Fontal Aina, Beatriz
Trapero Candela, Carla
Rojo Fité, Nuria
Rico, Inma
Campdelacreu i Fumadó, Jaume
Fowler, Cristopher
Laws, Simon M.
Tort Merino, Adrià
Sánchez del Valle Díaz, Raquel
Bello, Joan
Fortea Ormaechea, Juan
Lleó Bisa, Alberto
Mehanian, Courosh
Swerdlow, Russell H.
Reñé Ramírez, Ramon
Barrachina, Marta
author_role author
author2 Mosquera Mayo, José Luís
Blanch Lozano, Marta
Martí Benaiges, Pau
Fontal Aina, Beatriz
Trapero Candela, Carla
Rojo Fité, Nuria
Rico, Inma
Campdelacreu i Fumadó, Jaume
Fowler, Cristopher
Laws, Simon M.
Tort Merino, Adrià
Sánchez del Valle Díaz, Raquel
Bello, Joan
Fortea Ormaechea, Juan
Lleó Bisa, Alberto
Mehanian, Courosh
Swerdlow, Russell H.
Reñé Ramírez, Ramon
Barrachina, Marta
author2_role author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
dc.subject.none.fl_str_mv ADN mitocondrial
Malaltia d'Alzheimer
Neurociències
Metilació
Neurologia
Mitochondrial DNA
Alzheimer's disease
Neurosciences
Methylation
Neurology
topic ADN mitocondrial
Malaltia d'Alzheimer
Neurociències
Metilació
Neurologia
Mitochondrial DNA
Alzheimer's disease
Neurosciences
Methylation
Neurology
description Alzheimer's Disease Dementia (ADD) prognosis is an unmet medical need. Mitochondrial dysfunction is an early AD etiopathogenic factor. The present study analyzed mitochondrial DNA (mtDNA) methylation patterns in blood samples from patients with mild cognitive impairment (MCI) who progressed to ADD (P), MCI remained stable (NP), and Cognitively Normal (CN) individuals. Differentially methylated sites were identified in the D-loop region in both CN vs. NP and NP vs. P comparisons, even before β-amyloid positivity. A Random Forest model was developed using mtDNA methylation data combined with cognitive and risk factor features. Model's performance was assessed by cross-validation and tested on an independent set, achieving 84.4% accuracy in training and 83.2% (95% CI: 75.2%-89.4%) in testing. For identifying P patients, sensitivity and specificity were 95.1% and 70.7%, respectively. The AUC-ROC was 90.3%. The developed model demonstrates predictive capacity in distinguishing cognitive decline and stability in MCI individuals, independently of their β-amyloid status.
publishDate 2025
dc.date.none.fl_str_mv 2025
dc.type.none.fl_str_mv info:eu-repo/semantics/article
info:eu-repo/semantics/publishedVersion
format article
status_str publishedVersion
dc.identifier.none.fl_str_mv https://hdl.handle.net/2445/224918
url https://hdl.handle.net/2445/224918
dc.language.none.fl_str_mv Inglés
language_invalid_str_mv Inglés
dc.relation.none.fl_str_mv Reproducció del document publicat a: https://doi.org/10.1016/j.isci.2025.113418
iScience, 2025, vol. 28, num. 9, 113418
https://doi.org/10.1016/j.isci.2025.113418
dc.rights.none.fl_str_mv cc-by-nc-nd (c) Gascón-Bayarri, Jordi. et al., 2025
http://creativecommons.org/licenses/by-nc-nd/4.0/
info:eu-repo/semantics/openAccess
rights_invalid_str_mv cc-by-nc-nd (c) Gascón-Bayarri, Jordi. et al., 2025
http://creativecommons.org/licenses/by-nc-nd/4.0/
eu_rights_str_mv openAccess
dc.format.none.fl_str_mv application/pdf
dc.publisher.none.fl_str_mv Elsevier
publisher.none.fl_str_mv Elsevier
dc.source.none.fl_str_mv Articles publicats en revistes (Medicina)
reponame:Dipòsit Digital de la UB
instname:Universidad de Barcelona
instname_str Universidad de Barcelona
reponame_str Dipòsit Digital de la UB
collection Dipòsit Digital de la UB
repository.name.fl_str_mv
repository.mail.fl_str_mv
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