Pegcetacoplan in idiopathic and familial pediatric C3 glomerulopathy

C3 glomerulopathy (C3G) and immune complex-mediated membranoproliferative glomerulonephritis (IC-MPGN) represent a continuous spectrum of a glomerular disease driven by dysregulation of the complement and characterized by C3 deposition alone or associated with immunoglobulins. Despite the significan...

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Detalles Bibliográficos
Autores: Román Ortiz, Elena, Sáez Bello, Marina, Reparaz Suevos, Andrea, Perez Ebri, Marisa, Aguilar Bacallado, Francisco, LLopis Salvia, Pilar, Climente Martí, Mónica, Rodríguez de Córdoba, Santiago
Tipo de recurso: artículo
Estado:Versión publicada
Fecha de publicación:2025
País:España
Institución:Consejo Superior de Investigaciones Científicas (CSIC)
Repositorio:DIGITAL.CSIC. Repositorio Institucional del CSIC
OAI Identifier:oai:digital.csic.es:10261/413115
Acceso en línea:http://hdl.handle.net/10261/413115
https://api.elsevier.com/content/abstract/scopus_id/105024350084
Access Level:acceso abierto
Palabra clave:C3 glomerulonephritis
C3 glomerulopathy
C3 inhibitor
Children
Complement
Pegcetacoplan
Descripción
Sumario:C3 glomerulopathy (C3G) and immune complex-mediated membranoproliferative glomerulonephritis (IC-MPGN) represent a continuous spectrum of a glomerular disease driven by dysregulation of the complement and characterized by C3 deposition alone or associated with immunoglobulins. Despite the significant burden and poor prognosis associated with these conditions, no therapies have been approved for their treatment in children.