Self-assembling, supramolecular chemistry and pharmacology of amphotericin B: Poly-aggregates, oligomers and monomers

Chemicals and CAS Registry Numbers amphotericin B 1397-89-3, 30652-87-0 deoxycholate sodium 302-95-4 ergosterol 23637-22-1, 2418-45-3, 3992-98-1, 57-87-4 gamma cyclodextrin 17465-86-0 sodium dihydrogen phosphate 7558-80-7, 7632-05-5 deoxycholic acid 83-44-3 Amphotericin B Antifungal Agents Deoxychol...

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Autores: Fernández-García, Raquel, Muñoz-García, Juan C., Wallace, Matthew, Fabian, Laszlo, González-Burgos, Elena, Gómez-Serranillos, M Pilar, Raposo, Rafaela, Bolás-Fernández, Francisco, Ballesteros, M Paloma, Healy, Anne Marie, Khimyak, Yaroslav Z, Serrano, Dolores R
Tipo de recurso: artículo
Estado:Versión aceptada para publicación
Fecha de publicación:2022
País:España
Institución:Consejo Superior de Investigaciones Científicas (CSIC)
Repositorio:DIGITAL.CSIC. Repositorio Institucional del CSIC
OAI Identifier:oai:digital.csic.es:10261/394812
Acceso en línea:http://hdl.handle.net/10261/394812
https://api.elsevier.com/content/abstract/scopus_id/85121557127
Access Level:acceso abierto
Palabra clave:Supramolecular chemistry
Aggregation states
Amphotericin B
NMR
Oligomer
Poly-aggregate
ROS
Self-assembly
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oai_identifier_str oai:digital.csic.es:10261/394812
network_acronym_str ES
network_name_str España
repository_id_str
dc.title.none.fl_str_mv Self-assembling, supramolecular chemistry and pharmacology of amphotericin B: Poly-aggregates, oligomers and monomers
title Self-assembling, supramolecular chemistry and pharmacology of amphotericin B: Poly-aggregates, oligomers and monomers
spellingShingle Self-assembling, supramolecular chemistry and pharmacology of amphotericin B: Poly-aggregates, oligomers and monomers
Fernández-García, Raquel
Supramolecular chemistry
Aggregation states
Amphotericin B
NMR
Oligomer
Poly-aggregate
ROS
Self-assembly
title_short Self-assembling, supramolecular chemistry and pharmacology of amphotericin B: Poly-aggregates, oligomers and monomers
title_full Self-assembling, supramolecular chemistry and pharmacology of amphotericin B: Poly-aggregates, oligomers and monomers
title_fullStr Self-assembling, supramolecular chemistry and pharmacology of amphotericin B: Poly-aggregates, oligomers and monomers
title_full_unstemmed Self-assembling, supramolecular chemistry and pharmacology of amphotericin B: Poly-aggregates, oligomers and monomers
title_sort Self-assembling, supramolecular chemistry and pharmacology of amphotericin B: Poly-aggregates, oligomers and monomers
dc.creator.none.fl_str_mv Fernández-García, Raquel
Muñoz-García, Juan C.
Wallace, Matthew
Fabian, Laszlo
González-Burgos, Elena
Gómez-Serranillos, M Pilar
Raposo, Rafaela
Bolás-Fernández, Francisco
Ballesteros, M Paloma
Healy, Anne Marie
Khimyak, Yaroslav Z
Serrano, Dolores R
author Fernández-García, Raquel
author_facet Fernández-García, Raquel
Muñoz-García, Juan C.
Wallace, Matthew
Fabian, Laszlo
González-Burgos, Elena
Gómez-Serranillos, M Pilar
Raposo, Rafaela
Bolás-Fernández, Francisco
Ballesteros, M Paloma
Healy, Anne Marie
Khimyak, Yaroslav Z
Serrano, Dolores R
author_role author
author2 Muñoz-García, Juan C.
Wallace, Matthew
Fabian, Laszlo
González-Burgos, Elena
Gómez-Serranillos, M Pilar
Raposo, Rafaela
Bolás-Fernández, Francisco
Ballesteros, M Paloma
Healy, Anne Marie
Khimyak, Yaroslav Z
Serrano, Dolores R
author2_role author
author
author
author
author
author
author
author
author
author
author
dc.contributor.none.fl_str_mv Boehringer Ingelheim Fonds
Trinity College Dublin
University of East Anglia
Science Foundation Ireland
European Commission
Royal Society (UK)
UK Research and Innovation
Engineering and Physical Sciences Research Council (UK)
European Society of Clinical Microbiology and Infectious Diseases
Fernández-García, Raquel [0000-0001-5505-2615]
Muñoz-García, Juan C. [0000-0003-2246-3236]
Wallace, Matthew [0000-0002-5751-1827]
Fabian, Laszlo [0000-0002-2087-4501]
González-Burgos, Elena [0000-0003-2119-8768]
Gómez-Serranillos, M Pilar [0000-0002-9178-3420]
Raposo, Rafaela [0000-0002-2941-9767]
Bolás-Fernández, Francisco [0000-0001-8062-2974]
Ballesteros, M Paloma [0009-0003-9917-2506]
Healy, Anne Marie [0000-0001-5093-9786]
Khimyak, Yaroslav Z [0000-0003-0424-4128]
Serrano, Dolores R [0000-0002-0475-8420]
dc.subject.none.fl_str_mv Supramolecular chemistry
Aggregation states
Amphotericin B
NMR
Oligomer
Poly-aggregate
ROS
Self-assembly
topic Supramolecular chemistry
Aggregation states
Amphotericin B
NMR
Oligomer
Poly-aggregate
ROS
Self-assembly
description Chemicals and CAS Registry Numbers amphotericin B 1397-89-3, 30652-87-0 deoxycholate sodium 302-95-4 ergosterol 23637-22-1, 2418-45-3, 3992-98-1, 57-87-4 gamma cyclodextrin 17465-86-0 sodium dihydrogen phosphate 7558-80-7, 7632-05-5 deoxycholic acid 83-44-3 Amphotericin B Antifungal Agents Deoxycholic Acid Ergosterol Phospholipids
publishDate 2022
dc.date.none.fl_str_mv 2022
2025
2025
dc.type.none.fl_str_mv info:eu-repo/semantics/article
http://purl.org/coar/resource_type/c_6501
Postprint
info:eu-repo/semantics/acceptedVersion
format article
status_str acceptedVersion
dc.identifier.none.fl_str_mv http://hdl.handle.net/10261/394812
https://api.elsevier.com/content/abstract/scopus_id/85121557127
url http://hdl.handle.net/10261/394812
https://api.elsevier.com/content/abstract/scopus_id/85121557127
dc.language.none.fl_str_mv Inglés
language_invalid_str_mv Inglés
dc.relation.none.fl_str_mv #PLACEHOLDER_PARENT_METADATA_VALUE#
#PLACEHOLDER_PARENT_METADATA_VALUE#
SFI/12/RC/2275
SFI/12/RC/2275_P2
https://doi.org/10.1016/j.jconrel.2021.12.019
No
dc.rights.none.fl_str_mv info:eu-repo/semantics/openAccess
eu_rights_str_mv openAccess
dc.format.none.fl_str_mv aplication/pdf
dc.publisher.none.fl_str_mv Elsevier BV
publisher.none.fl_str_mv Elsevier BV
dc.source.none.fl_str_mv reponame:DIGITAL.CSIC. Repositorio Institucional del CSIC
instname:Consejo Superior de Investigaciones Científicas (CSIC)
instname_str Consejo Superior de Investigaciones Científicas (CSIC)
reponame_str DIGITAL.CSIC. Repositorio Institucional del CSIC
collection DIGITAL.CSIC. Repositorio Institucional del CSIC
repository.name.fl_str_mv
repository.mail.fl_str_mv
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spelling Self-assembling, supramolecular chemistry and pharmacology of amphotericin B: Poly-aggregates, oligomers and monomersFernández-García, RaquelMuñoz-García, Juan C.Wallace, MatthewFabian, LaszloGonzález-Burgos, ElenaGómez-Serranillos, M PilarRaposo, RafaelaBolás-Fernández, FranciscoBallesteros, M PalomaHealy, Anne MarieKhimyak, Yaroslav ZSerrano, Dolores RSupramolecular chemistryAggregation statesAmphotericin BNMROligomerPoly-aggregateROSSelf-assemblyChemicals and CAS Registry Numbers amphotericin B 1397-89-3, 30652-87-0 deoxycholate sodium 302-95-4 ergosterol 23637-22-1, 2418-45-3, 3992-98-1, 57-87-4 gamma cyclodextrin 17465-86-0 sodium dihydrogen phosphate 7558-80-7, 7632-05-5 deoxycholic acid 83-44-3 Amphotericin B Antifungal Agents Deoxycholic Acid Ergosterol PhospholipidsAntifungal drugs such as amphotericin B (AmB) interact with lipids and phospholipids located on fungal cell membranes to disrupt them and create pores, leading to cell apoptosis and therefore efficacy. At the same time, the interaction can also take place with cell components from mammalian cells, leading to toxicity. AmB was selected as a model antifungal drug due to the complexity of its supramolecular chemical structure which can self-assemble in three different aggregation states in aqueous media: monomer, oligomer (also known as dimer) and poly-aggregate. The interplay between AmB self-assembly and its efficacy or toxicity against fungal or mammalian cells is not yet fully understood. To the best of our knowledge, this is the first report that investigates the role of excipients in the supramolecular chemistry of AmB and the impact on its biological activity and toxicity. The monomeric state was obtained by complexation with cyclodextrins resulting in the most toxic state, which was attributed to the greater production of highly reactive oxygen species upon disruption of mammalian cell membranes, a less specific mechanism of action compared to the binding to the ergosterol located in fungal cell membranes. The interaction between AmB and sodium deoxycholate resulted in the oligomeric and poly-aggregated forms which bound more selectively to the ergosterol of fungal cell membranes. NMR combined with XRD studies elucidated the interaction between drug and excipient to achieve the AmB aggregation states, and ultimately, their diffusivity across membranes. A linear correlation between particle size and the efficacy/toxicity ratio was established allowing to modulate the biological effect of the drug and hence, to improve pharmacological regimens. However, particle size is not the only factor modulating the biological response but also the equilibrium of each state which dictates the fraction of free monomeric form available. Tuning the aggregation state of AmB formulations is a promising strategy to trigger a more selective response against fungal cells and to reduce the toxicity in mammalian cells.R. Fernández-García acknowledges Boehringer Ingelheim Fonds for her travel grant to perform solid-state characterisation at Trinity College Dublin and Erasmus + programme Key Action 1 (KA1) for her scholarship to perform NMR experiments at University of East Anglia. A.M. Healy acknowledges Science Foundation Ireland grants co-funded under the European Regional Development Fund (SFI/12/RC/2275 and SFI/12/RC/2275_P2). M. Wallace thanks the Royal Commission for the Exhibition of 1851 for a Research Fellowship and the Royal Society for a Research Grant: RGS\R1\191336. This work was also supported by a UKRI Future Leaders Fellowship to M. Wallace (MR/T044020/1). The Engineering and Physical Sciences Research Council (EPSRC) is acknowledged for provision of financial support (EP/N033337/1) for J.C. Muñoz-García and Y.Z. Khimyak. We are grateful for the use of the University of East Anglia (UEA) Faculty of Science NMR facility. This study has been partially funded by a Research Grant [year 2021, ID: 16306] from the European Society of Clinical Microbiology and Infectious Diseases (ESCMID) to D.R. Serrano.Peer reviewedElsevier BVBoehringer Ingelheim FondsTrinity College DublinUniversity of East AngliaScience Foundation IrelandEuropean CommissionRoyal Society (UK)UK Research and InnovationEngineering and Physical Sciences Research Council (UK)European Society of Clinical Microbiology and Infectious DiseasesFernández-García, Raquel [0000-0001-5505-2615]Muñoz-García, Juan C. [0000-0003-2246-3236]Wallace, Matthew [0000-0002-5751-1827]Fabian, Laszlo [0000-0002-2087-4501]González-Burgos, Elena [0000-0003-2119-8768]Gómez-Serranillos, M Pilar [0000-0002-9178-3420]Raposo, Rafaela [0000-0002-2941-9767]Bolás-Fernández, Francisco [0000-0001-8062-2974]Ballesteros, M Paloma [0009-0003-9917-2506]Healy, Anne Marie [0000-0001-5093-9786]Khimyak, Yaroslav Z [0000-0003-0424-4128]Serrano, Dolores R [0000-0002-0475-8420]202520252022info:eu-repo/semantics/articlehttp://purl.org/coar/resource_type/c_6501Postprintinfo:eu-repo/semantics/acceptedVersionaplication/pdfhttp://hdl.handle.net/10261/394812https://api.elsevier.com/content/abstract/scopus_id/85121557127reponame:DIGITAL.CSIC. Repositorio Institucional del CSICinstname:Consejo Superior de Investigaciones Científicas (CSIC)Inglés#PLACEHOLDER_PARENT_METADATA_VALUE##PLACEHOLDER_PARENT_METADATA_VALUE#SFI/12/RC/2275SFI/12/RC/2275_P2https://doi.org/10.1016/j.jconrel.2021.12.019Noinfo:eu-repo/semantics/openAccessoai:digital.csic.es:10261/3948122026-05-22T06:33:51Z
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