Single-cell transcriptional profile of CD34+ hematopoietic progenitor cells from del(5q) myelodysplastic syndromes and impact of lenalidomide

While myelodysplastic syndromes with del(5q) (del(5q) MDS) comprises a well-defined hematological subgroup, the molecular basis underlying its origin remains unknown. Using single cell RNA-seq (scRNA-seq) on CD34+ progenitors from del(5q) MDS patients, we have identified cells harboring the deletion...

Descripción completa

Detalles Bibliográficos
Autores: Serrano-Sanz, G. (Guillermo)|||/items/5ed5047b-1ad7-44a2-8674-de750c97b7c5, Berastegui-Zufiaurre, N. (Nerea)|||/items/a609b1d4-fbed-4852-96eb-90e1cfe04e52, Díaz-Mazkiaran, A. (Aintzane)|||/items/8f723f6e-3569-43c9-ae70-07499bc3cac8, García-Olloqui, P. (Paula)|||/items/33aebcca-bf96-4a81-a74d-9fcd60b275cc, Rodriguez-Res, C. (Carmen)|||/items/99683585-e42d-4e7b-8031-93320beed7fd, Huerga-Dominguez, S. (Sofia)|||/items/a62c6e59-be71-4b34-b0b6-6deb286bbf3f, Ainciburu-Fernández, M. (Marina)|||/items/71018cd2-9706-4dd0-84a9-77a8d03fef99, Vilas-Zornoza, A. (Amaia)|||/items/7435672d-e471-4409-8325-006fef27fb12, San-Martín-Uriz, P. (Patxi)|||/items/621b7a74-311b-4ff1-b688-53d810e30429, Aguirre-Ruiz, P. (Paula)|||/items/fd10df63-1585-43c5-bb82-d4357a15e7d8, Ullate-Agote, A. (Asier)|||/items/af0561e9-aebe-4e94-9cb1-6bb3aa8bf975, Ariceta, B. (Beñat)|||/items/e0060bfb-843a-4b76-a474-b79c0eeec803, Lamo-de-Espinosa-Vázquez-de-Sola, J.M. (José María)|||/items/75feb837-6d53-41fe-808d-4b70661db44e, Acha, P. (Pamela)|||/items/7d12fe4a-6af1-41ff-8d28-87598f6ca8cb, Calvete, O. (Oriol)|||/items/a22ae40f-38fc-4588-ad08-a83629184206, Jimenez-Solas, T. (Tamara)|||/items/7a4dbe5e-7060-4c1d-b632-9dd5089fe072, Molero, A. (Antonieta)|||/items/ea2d4363-f7f8-4859-b4f8-bf034d96ed9e, Montoro-Gómez, M.J. (Maria Julia)|||/items/9bd28e22-a47c-43ed-9001-e3e5c95aebec, Diez-Campelo, M. (Maria)|||/items/80adaceb-3fc4-44c2-bba0-2c88e6400317, Valcarcel, D. (David)|||/items/672eb58a-39da-45ab-85d2-58b2496cd1ab, Sole, F. (Francisco)|||/items/cb283076-40b1-4363-81ee-5275088886bf, Alfonso-Piérola, A. (Ana)|||/items/0212a5e6-923f-42aa-8ba3-b0ce4e1d6e10, Prosper-Cardoso, F. (Felipe)|||/items/3d1b0b82-06c3-4e63-8280-e903dc4dc0c1, Ezponda-Itoiz, T. (Teresa)|||/items/6941e85c-0814-4cde-9237-84a06fbf1697, Hernaez-Arrazola, M. (Mikel)|||/items/954a4ee7-b04c-4dc5-9bfc-7a48332c7e5a, Ochoa-Álvarez, I. (Idoia)|||/items/6326dacc-419f-4156-a9c3-9e79cfcc6a3c
Tipo de recurso: artículo
Fecha de publicación:2024
País:España
Institución:Universidad de Navarra
Repositorio:Dadun. Depósito Académico Digital de la Universidad de Navarra
Idioma:inglés
OAI Identifier:oai:dadun.unav.edu:10171/113241
Acceso en línea:https://hdl.handle.net/10171/113241
Access Level:acceso abierto
id ES_2aafbc151c9f6c8e6b3786c2da01d4ce
oai_identifier_str oai:dadun.unav.edu:10171/113241
network_acronym_str ES
network_name_str España
repository_id_str
spelling Single-cell transcriptional profile of CD34+ hematopoietic progenitor cells from del(5q) myelodysplastic syndromes and impact of lenalidomideSerrano-Sanz, G. (Guillermo)|||/items/5ed5047b-1ad7-44a2-8674-de750c97b7c5Berastegui-Zufiaurre, N. (Nerea)|||/items/a609b1d4-fbed-4852-96eb-90e1cfe04e52Díaz-Mazkiaran, A. (Aintzane)|||/items/8f723f6e-3569-43c9-ae70-07499bc3cac8García-Olloqui, P. (Paula)|||/items/33aebcca-bf96-4a81-a74d-9fcd60b275ccRodriguez-Res, C. (Carmen)|||/items/99683585-e42d-4e7b-8031-93320beed7fdHuerga-Dominguez, S. (Sofia)|||/items/a62c6e59-be71-4b34-b0b6-6deb286bbf3fAinciburu-Fernández, M. (Marina)|||/items/71018cd2-9706-4dd0-84a9-77a8d03fef99Vilas-Zornoza, A. (Amaia)|||/items/7435672d-e471-4409-8325-006fef27fb12San-Martín-Uriz, P. (Patxi)|||/items/621b7a74-311b-4ff1-b688-53d810e30429Aguirre-Ruiz, P. (Paula)|||/items/fd10df63-1585-43c5-bb82-d4357a15e7d8Ullate-Agote, A. (Asier)|||/items/af0561e9-aebe-4e94-9cb1-6bb3aa8bf975Ariceta, B. (Beñat)|||/items/e0060bfb-843a-4b76-a474-b79c0eeec803Lamo-de-Espinosa-Vázquez-de-Sola, J.M. (José María)|||/items/75feb837-6d53-41fe-808d-4b70661db44eAcha, P. (Pamela)|||/items/7d12fe4a-6af1-41ff-8d28-87598f6ca8cbCalvete, O. (Oriol)|||/items/a22ae40f-38fc-4588-ad08-a83629184206Jimenez-Solas, T. (Tamara)|||/items/7a4dbe5e-7060-4c1d-b632-9dd5089fe072Molero, A. (Antonieta)|||/items/ea2d4363-f7f8-4859-b4f8-bf034d96ed9eMontoro-Gómez, M.J. (Maria Julia)|||/items/9bd28e22-a47c-43ed-9001-e3e5c95aebecDiez-Campelo, M. (Maria)|||/items/80adaceb-3fc4-44c2-bba0-2c88e6400317Valcarcel, D. (David)|||/items/672eb58a-39da-45ab-85d2-58b2496cd1abSole, F. (Francisco)|||/items/cb283076-40b1-4363-81ee-5275088886bfAlfonso-Piérola, A. (Ana)|||/items/0212a5e6-923f-42aa-8ba3-b0ce4e1d6e10Prosper-Cardoso, F. (Felipe)|||/items/3d1b0b82-06c3-4e63-8280-e903dc4dc0c1Ezponda-Itoiz, T. (Teresa)|||/items/6941e85c-0814-4cde-9237-84a06fbf1697Hernaez-Arrazola, M. (Mikel)|||/items/954a4ee7-b04c-4dc5-9bfc-7a48332c7e5aOchoa-Álvarez, I. (Idoia)|||/items/6326dacc-419f-4156-a9c3-9e79cfcc6a3cWhile myelodysplastic syndromes with del(5q) (del(5q) MDS) comprises a well-defined hematological subgroup, the molecular basis underlying its origin remains unknown. Using single cell RNA-seq (scRNA-seq) on CD34+ progenitors from del(5q) MDS patients, we have identified cells harboring the deletion, characterizing the transcriptional impact of this genetic insult on disease pathogenesis and treatment response. Interestingly, both del(5q) and non-del(5q) cells present similar transcriptional lesions, indicating that all cells, and not only those harboring the deletion, may contribute to aberrant hematopoietic differentiation. However, gene regulatory network (GRN) analyses reveal a group of regulons showing aberrant activity that could trigger altered hematopoiesis exclusively in del(5q) cells, pointing to a more prominent role of these cells in disease phenotype. In del(5q) MDS patients achieving hematological response upon lenalidomide treatment, the drug reverts several transcriptional alterations in both del(5q) and non-del(5q) cells, but other lesions remain, which may be responsible for potential future relapses. Moreover, lack of hematological response is associated with the inability of lenalidomide to reverse transcriptional alterations. Collectively, this study reveals transcriptional alterations that could contribute to the pathogenesis and treatment response of del(5q) MDS.Nature ResearchDadun. Depósito Académico Digital Universidad de Navarra20242024-01-0120242024-01-01journal articlehttp://purl.org/coar/resource_type/c_6501info:eu-repo/semantics/articleapplication/pdfhttps://hdl.handle.net/10171/113241reponame:Dadun. Depósito Académico Digital de la Universidad de Navarrainstname:Universidad de NavarraInglésengopen accesshttp://purl.org/coar/access_right/c_abf2info:eu-repo/semantics/openAccessoai:dadun.unav.edu:10171/1132412026-06-21T12:47:57Z
dc.title.none.fl_str_mv Single-cell transcriptional profile of CD34+ hematopoietic progenitor cells from del(5q) myelodysplastic syndromes and impact of lenalidomide
title Single-cell transcriptional profile of CD34+ hematopoietic progenitor cells from del(5q) myelodysplastic syndromes and impact of lenalidomide
spellingShingle Single-cell transcriptional profile of CD34+ hematopoietic progenitor cells from del(5q) myelodysplastic syndromes and impact of lenalidomide
Serrano-Sanz, G. (Guillermo)|||/items/5ed5047b-1ad7-44a2-8674-de750c97b7c5
title_short Single-cell transcriptional profile of CD34+ hematopoietic progenitor cells from del(5q) myelodysplastic syndromes and impact of lenalidomide
title_full Single-cell transcriptional profile of CD34+ hematopoietic progenitor cells from del(5q) myelodysplastic syndromes and impact of lenalidomide
title_fullStr Single-cell transcriptional profile of CD34+ hematopoietic progenitor cells from del(5q) myelodysplastic syndromes and impact of lenalidomide
title_full_unstemmed Single-cell transcriptional profile of CD34+ hematopoietic progenitor cells from del(5q) myelodysplastic syndromes and impact of lenalidomide
title_sort Single-cell transcriptional profile of CD34+ hematopoietic progenitor cells from del(5q) myelodysplastic syndromes and impact of lenalidomide
dc.creator.none.fl_str_mv Serrano-Sanz, G. (Guillermo)|||/items/5ed5047b-1ad7-44a2-8674-de750c97b7c5
Berastegui-Zufiaurre, N. (Nerea)|||/items/a609b1d4-fbed-4852-96eb-90e1cfe04e52
Díaz-Mazkiaran, A. (Aintzane)|||/items/8f723f6e-3569-43c9-ae70-07499bc3cac8
García-Olloqui, P. (Paula)|||/items/33aebcca-bf96-4a81-a74d-9fcd60b275cc
Rodriguez-Res, C. (Carmen)|||/items/99683585-e42d-4e7b-8031-93320beed7fd
Huerga-Dominguez, S. (Sofia)|||/items/a62c6e59-be71-4b34-b0b6-6deb286bbf3f
Ainciburu-Fernández, M. (Marina)|||/items/71018cd2-9706-4dd0-84a9-77a8d03fef99
Vilas-Zornoza, A. (Amaia)|||/items/7435672d-e471-4409-8325-006fef27fb12
San-Martín-Uriz, P. (Patxi)|||/items/621b7a74-311b-4ff1-b688-53d810e30429
Aguirre-Ruiz, P. (Paula)|||/items/fd10df63-1585-43c5-bb82-d4357a15e7d8
Ullate-Agote, A. (Asier)|||/items/af0561e9-aebe-4e94-9cb1-6bb3aa8bf975
Ariceta, B. (Beñat)|||/items/e0060bfb-843a-4b76-a474-b79c0eeec803
Lamo-de-Espinosa-Vázquez-de-Sola, J.M. (José María)|||/items/75feb837-6d53-41fe-808d-4b70661db44e
Acha, P. (Pamela)|||/items/7d12fe4a-6af1-41ff-8d28-87598f6ca8cb
Calvete, O. (Oriol)|||/items/a22ae40f-38fc-4588-ad08-a83629184206
Jimenez-Solas, T. (Tamara)|||/items/7a4dbe5e-7060-4c1d-b632-9dd5089fe072
Molero, A. (Antonieta)|||/items/ea2d4363-f7f8-4859-b4f8-bf034d96ed9e
Montoro-Gómez, M.J. (Maria Julia)|||/items/9bd28e22-a47c-43ed-9001-e3e5c95aebec
Diez-Campelo, M. (Maria)|||/items/80adaceb-3fc4-44c2-bba0-2c88e6400317
Valcarcel, D. (David)|||/items/672eb58a-39da-45ab-85d2-58b2496cd1ab
Sole, F. (Francisco)|||/items/cb283076-40b1-4363-81ee-5275088886bf
Alfonso-Piérola, A. (Ana)|||/items/0212a5e6-923f-42aa-8ba3-b0ce4e1d6e10
Prosper-Cardoso, F. (Felipe)|||/items/3d1b0b82-06c3-4e63-8280-e903dc4dc0c1
Ezponda-Itoiz, T. (Teresa)|||/items/6941e85c-0814-4cde-9237-84a06fbf1697
Hernaez-Arrazola, M. (Mikel)|||/items/954a4ee7-b04c-4dc5-9bfc-7a48332c7e5a
Ochoa-Álvarez, I. (Idoia)|||/items/6326dacc-419f-4156-a9c3-9e79cfcc6a3c
author Serrano-Sanz, G. (Guillermo)|||/items/5ed5047b-1ad7-44a2-8674-de750c97b7c5
author_facet Serrano-Sanz, G. (Guillermo)|||/items/5ed5047b-1ad7-44a2-8674-de750c97b7c5
Berastegui-Zufiaurre, N. (Nerea)|||/items/a609b1d4-fbed-4852-96eb-90e1cfe04e52
Díaz-Mazkiaran, A. (Aintzane)|||/items/8f723f6e-3569-43c9-ae70-07499bc3cac8
García-Olloqui, P. (Paula)|||/items/33aebcca-bf96-4a81-a74d-9fcd60b275cc
Rodriguez-Res, C. (Carmen)|||/items/99683585-e42d-4e7b-8031-93320beed7fd
Huerga-Dominguez, S. (Sofia)|||/items/a62c6e59-be71-4b34-b0b6-6deb286bbf3f
Ainciburu-Fernández, M. (Marina)|||/items/71018cd2-9706-4dd0-84a9-77a8d03fef99
Vilas-Zornoza, A. (Amaia)|||/items/7435672d-e471-4409-8325-006fef27fb12
San-Martín-Uriz, P. (Patxi)|||/items/621b7a74-311b-4ff1-b688-53d810e30429
Aguirre-Ruiz, P. (Paula)|||/items/fd10df63-1585-43c5-bb82-d4357a15e7d8
Ullate-Agote, A. (Asier)|||/items/af0561e9-aebe-4e94-9cb1-6bb3aa8bf975
Ariceta, B. (Beñat)|||/items/e0060bfb-843a-4b76-a474-b79c0eeec803
Lamo-de-Espinosa-Vázquez-de-Sola, J.M. (José María)|||/items/75feb837-6d53-41fe-808d-4b70661db44e
Acha, P. (Pamela)|||/items/7d12fe4a-6af1-41ff-8d28-87598f6ca8cb
Calvete, O. (Oriol)|||/items/a22ae40f-38fc-4588-ad08-a83629184206
Jimenez-Solas, T. (Tamara)|||/items/7a4dbe5e-7060-4c1d-b632-9dd5089fe072
Molero, A. (Antonieta)|||/items/ea2d4363-f7f8-4859-b4f8-bf034d96ed9e
Montoro-Gómez, M.J. (Maria Julia)|||/items/9bd28e22-a47c-43ed-9001-e3e5c95aebec
Diez-Campelo, M. (Maria)|||/items/80adaceb-3fc4-44c2-bba0-2c88e6400317
Valcarcel, D. (David)|||/items/672eb58a-39da-45ab-85d2-58b2496cd1ab
Sole, F. (Francisco)|||/items/cb283076-40b1-4363-81ee-5275088886bf
Alfonso-Piérola, A. (Ana)|||/items/0212a5e6-923f-42aa-8ba3-b0ce4e1d6e10
Prosper-Cardoso, F. (Felipe)|||/items/3d1b0b82-06c3-4e63-8280-e903dc4dc0c1
Ezponda-Itoiz, T. (Teresa)|||/items/6941e85c-0814-4cde-9237-84a06fbf1697
Hernaez-Arrazola, M. (Mikel)|||/items/954a4ee7-b04c-4dc5-9bfc-7a48332c7e5a
Ochoa-Álvarez, I. (Idoia)|||/items/6326dacc-419f-4156-a9c3-9e79cfcc6a3c
author_role author
author2 Berastegui-Zufiaurre, N. (Nerea)|||/items/a609b1d4-fbed-4852-96eb-90e1cfe04e52
Díaz-Mazkiaran, A. (Aintzane)|||/items/8f723f6e-3569-43c9-ae70-07499bc3cac8
García-Olloqui, P. (Paula)|||/items/33aebcca-bf96-4a81-a74d-9fcd60b275cc
Rodriguez-Res, C. (Carmen)|||/items/99683585-e42d-4e7b-8031-93320beed7fd
Huerga-Dominguez, S. (Sofia)|||/items/a62c6e59-be71-4b34-b0b6-6deb286bbf3f
Ainciburu-Fernández, M. (Marina)|||/items/71018cd2-9706-4dd0-84a9-77a8d03fef99
Vilas-Zornoza, A. (Amaia)|||/items/7435672d-e471-4409-8325-006fef27fb12
San-Martín-Uriz, P. (Patxi)|||/items/621b7a74-311b-4ff1-b688-53d810e30429
Aguirre-Ruiz, P. (Paula)|||/items/fd10df63-1585-43c5-bb82-d4357a15e7d8
Ullate-Agote, A. (Asier)|||/items/af0561e9-aebe-4e94-9cb1-6bb3aa8bf975
Ariceta, B. (Beñat)|||/items/e0060bfb-843a-4b76-a474-b79c0eeec803
Lamo-de-Espinosa-Vázquez-de-Sola, J.M. (José María)|||/items/75feb837-6d53-41fe-808d-4b70661db44e
Acha, P. (Pamela)|||/items/7d12fe4a-6af1-41ff-8d28-87598f6ca8cb
Calvete, O. (Oriol)|||/items/a22ae40f-38fc-4588-ad08-a83629184206
Jimenez-Solas, T. (Tamara)|||/items/7a4dbe5e-7060-4c1d-b632-9dd5089fe072
Molero, A. (Antonieta)|||/items/ea2d4363-f7f8-4859-b4f8-bf034d96ed9e
Montoro-Gómez, M.J. (Maria Julia)|||/items/9bd28e22-a47c-43ed-9001-e3e5c95aebec
Diez-Campelo, M. (Maria)|||/items/80adaceb-3fc4-44c2-bba0-2c88e6400317
Valcarcel, D. (David)|||/items/672eb58a-39da-45ab-85d2-58b2496cd1ab
Sole, F. (Francisco)|||/items/cb283076-40b1-4363-81ee-5275088886bf
Alfonso-Piérola, A. (Ana)|||/items/0212a5e6-923f-42aa-8ba3-b0ce4e1d6e10
Prosper-Cardoso, F. (Felipe)|||/items/3d1b0b82-06c3-4e63-8280-e903dc4dc0c1
Ezponda-Itoiz, T. (Teresa)|||/items/6941e85c-0814-4cde-9237-84a06fbf1697
Hernaez-Arrazola, M. (Mikel)|||/items/954a4ee7-b04c-4dc5-9bfc-7a48332c7e5a
Ochoa-Álvarez, I. (Idoia)|||/items/6326dacc-419f-4156-a9c3-9e79cfcc6a3c
author2_role author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
dc.contributor.none.fl_str_mv Dadun. Depósito Académico Digital Universidad de Navarra
description While myelodysplastic syndromes with del(5q) (del(5q) MDS) comprises a well-defined hematological subgroup, the molecular basis underlying its origin remains unknown. Using single cell RNA-seq (scRNA-seq) on CD34+ progenitors from del(5q) MDS patients, we have identified cells harboring the deletion, characterizing the transcriptional impact of this genetic insult on disease pathogenesis and treatment response. Interestingly, both del(5q) and non-del(5q) cells present similar transcriptional lesions, indicating that all cells, and not only those harboring the deletion, may contribute to aberrant hematopoietic differentiation. However, gene regulatory network (GRN) analyses reveal a group of regulons showing aberrant activity that could trigger altered hematopoiesis exclusively in del(5q) cells, pointing to a more prominent role of these cells in disease phenotype. In del(5q) MDS patients achieving hematological response upon lenalidomide treatment, the drug reverts several transcriptional alterations in both del(5q) and non-del(5q) cells, but other lesions remain, which may be responsible for potential future relapses. Moreover, lack of hematological response is associated with the inability of lenalidomide to reverse transcriptional alterations. Collectively, this study reveals transcriptional alterations that could contribute to the pathogenesis and treatment response of del(5q) MDS.
publishDate 2024
dc.date.none.fl_str_mv 2024
2024-01-01
2024
2024-01-01
dc.type.none.fl_str_mv journal article
http://purl.org/coar/resource_type/c_6501
dc.type.openaire.fl_str_mv info:eu-repo/semantics/article
format article
dc.identifier.none.fl_str_mv https://hdl.handle.net/10171/113241
url https://hdl.handle.net/10171/113241
dc.language.none.fl_str_mv Inglés
eng
language_invalid_str_mv Inglés
language eng
dc.rights.none.fl_str_mv open access
http://purl.org/coar/access_right/c_abf2
dc.rights.openaire.fl_str_mv info:eu-repo/semantics/openAccess
rights_invalid_str_mv open access
http://purl.org/coar/access_right/c_abf2
eu_rights_str_mv openAccess
dc.format.none.fl_str_mv application/pdf
dc.publisher.none.fl_str_mv Nature Research
publisher.none.fl_str_mv Nature Research
dc.source.none.fl_str_mv reponame:Dadun. Depósito Académico Digital de la Universidad de Navarra
instname:Universidad de Navarra
instname_str Universidad de Navarra
reponame_str Dadun. Depósito Académico Digital de la Universidad de Navarra
collection Dadun. Depósito Académico Digital de la Universidad de Navarra
repository.name.fl_str_mv
repository.mail.fl_str_mv
_version_ 1869405088089374720
score 15,811543