Familial Dilated Cardiomyopathy and Sudden Cardiac Arrest: New Association with a SCN5A Mutation

Dilated cardiomyopathy (DCM) has significant morbidity and mortality. Familial transmission is reported in 20-35% of cases, highlighting the role of genetics in this disorder. We present an interesting family in which the index case is a 64-year-old woman who survived a sudden cardiac arrest. She pr...

Descripción completa

Detalles Bibliográficos
Autores: Rico, Yolanda, Ramis, Maria Francisca, Massot, Montse, Torres-Juan, Laura, Pons, Jaume, Fortuny Frau, Elena, Ripoll-Vera, Tomas, Gonzalez, Rosa, Peral, Vicente, Rosselló, Xavier, Heine-Suñer, Damián
Tipo de recurso: artículo
Fecha de publicación:2021
País:España
Institución:Instituto de Salud Carlos III (ISCIII)
Repositorio:Repisalud
Idioma:inglés
OAI Identifier:oai:repisalud.isciii.es:20.500.12105/23269
Acceso en línea:https://hdl.handle.net/20.500.12105/23269
Access Level:acceso abierto
Palabra clave:Dilated cardiomyopathy
Familial dilated cardiomyopathy
Genetic study
SCN5A
Novel mutation
Muerte Súbita Cardíaca
Predisposición Genética a la Enfermedad
Femenino
Mutación
Masculino
Cardiomiopatía Dilatada
Humanos
Persona de Mediana Edad
Pruebas Genéticas
Heterocigoto
Fenotipo
Linaje
Estudios Retrospectivos
Genetic Predisposition to Disease
Genetic Testing
Cardiomyopathy, Dilated
Humans
Heterozygote
Middle Aged
Phenotype
Male
Death, Sudden, Cardiac
Mutation
Female
Pedigree
Retrospective Studies
Descripción
Sumario:Dilated cardiomyopathy (DCM) has significant morbidity and mortality. Familial transmission is reported in 20-35% of cases, highlighting the role of genetics in this disorder. We present an interesting family in which the index case is a 64-year-old woman who survived a sudden cardiac arrest. She presented left ventricular dilatation and dysfunction, which indicated the presence of DCM, as well as a history of DCM and sudden arrest in her family (mother and sister). Genetic testing identified a heterozygous mutation c.74A > G missense change that causes an amino acid, p.Glu25Gly, change in the N-terminal domain of the SCN5A protein. After performing an exhaustive family medical history, we found that this previously not described mutation segregated within the family. All relatives with the DCM phenotype were carriers, whereas none of the noncarriers showed signs of heart disease, so this mutation is the most likely cause of the disease. This is the first time that a variant in the N-terminal domain of SCN5A has been associated with DCM.