Alcoholic Foamy Degeneration, an Entity Resembling Alcohol-Associated Hepatitis: Diagnosis, Prognosis, and Molecular Profiling

Background & aims: Alcoholic foamy degeneration (AFD) is a condition with similar clinical presentation to alcohol-associated hepatitis (AH), but with a specific histologic pattern. Information regarding the prevalence and prognosis of AFD is scarce and there are no tools for a noninvasive diagn...

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Autores: Gratacós-Ginès, Jordi, Avitabile, Emma, Montironi, Carla, Guillamon Thiery, Alex, Hernández Évole, Helena, Moreta, Maria José, Blaya, Delia, Ariño, Silvia, Rubio, A.B., Pérez-Guasch, Martina, Cervera, Marta, Carol, Marta, Fabrellas i Padrès, Núria, Soria, Anna, Juanola Mayos, Adrià, Graupera, Isabel, Sancho-Bru, Pau, Díaz Lorca, Maria Alba, Coll, Mar, Bataller, R., Ginès i Gibert, Pere, Pose Méndez, Elisa
Formato: artículo
Estado:Versión publicada
Fecha de publicación:2024
País:España
Recursos:Varias* (Consorci de Biblioteques Universitáries de Catalunya, Centre de Serveis Científics i Acadèmics de Catalunya)
Repositorio:Recercat. Dipósit de la Recerca de Catalunya
OAI Identifier:oai:recercat.cat:2445/217535
Acesso em linha:https://hdl.handle.net/2445/217535
Access Level:acceso abierto
Palavra-chave:Hepatopaties alcohòliques
Biòpsia
Histologia
Supervivència
Triglicèrids
Alcoholic liver diseases
Biopsy
Histology
Survival
Triglycerides
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spelling Alcoholic Foamy Degeneration, an Entity Resembling Alcohol-Associated Hepatitis: Diagnosis, Prognosis, and Molecular ProfilingGratacós-Ginès, JordiAvitabile, EmmaMontironi, CarlaGuillamon Thiery, AlexHernández Évole, HelenaMoreta, Maria JoséBlaya, DeliaAriño, SilviaRubio, A.B.Pérez-Guasch, MartinaCervera, MartaCarol, MartaFabrellas i Padrès, NúriaSoria, AnnaJuanola Mayos, AdriàGraupera, IsabelSancho-Bru, PauDíaz Lorca, Maria AlbaColl, MarBataller, R.Ginès i Gibert, PerePose Méndez, ElisaHepatopaties alcohòliquesBiòpsiaHistologiaSupervivènciaTriglicèridsAlcoholic liver diseasesBiopsyHistologySurvivalTriglyceridesBackground & aims: Alcoholic foamy degeneration (AFD) is a condition with similar clinical presentation to alcohol-associated hepatitis (AH), but with a specific histologic pattern. Information regarding the prevalence and prognosis of AFD is scarce and there are no tools for a noninvasive diagnosis. Methods: A cohort of patients admitted to the Hospital Clinic of Barcelona for clinical suspicion of AH who underwent liver biopsy was included. Patients were classified as AFD, AH, or other findings, according to histology. Clinical features, histology, and genetic expression of liver biopsy specimens were analyzed. The accuracy of National Institute on Alcohol Abuse and Alcoholism criteria and laboratory parameters for differential diagnosis were investigated. Results: Of 230 patients with a suspicion of AH, 18 (8%) met histologic criteria for AFD, 184 (80%) had definite AH, and 28 (12%) had other findings. In patients with AFD, massive steatosis was more frequent and the fibrosis stage was lower. AFD was characterized by down-regulation of liver fibrosis and inflammation genes and up-regulation of lipid metabolism and mitochondrial function genes. Patients with AFD had markedly better long-term survival (100% vs 57% in AFD vs AH; P = .002) despite not receiving corticosteroid treatment, even in a model for end-stage liver disease-matched sensitivity analysis. Serum triglyceride levels had an area under the receiver operating characteristic of 0.886 (95% CI, 0.807-0.964) for the diagnosis of AFD, whereas the National Institute on Alcohol Abuse and Alcoholism criteria performed poorly. A 1-step algorithm using triglyceride levels of 225 mg/dL (sensitivity, 0.77; specificity, 0.90; and Youden index, 0.67) is proposed for differential diagnosis. Conclusions: AFD in the setting of suspicion of AH is not uncommon. A differential diagnosis is important because prognosis and treatment differ largely. Triglyceride levels successfully identify most patients with AFD and may be helpful in decision making.Elsevier2025202520242025info:eu-repo/semantics/articleinfo:eu-repo/semantics/publishedVersion18 p.application/pdfhttps://hdl.handle.net/2445/217535Articles publicats en revistes (Fonaments Clínics)reponame:Recercat. Dipósit de la Recerca de Catalunyainstname:Varias* (Consorci de Biblioteques Universitáries de Catalunya, Centre de Serveis Científics i Acadèmics de Catalunya)InglésReproducció del document publicat a: https://doi.org/10.1016/j.cgh.2023.11.031Clinical Gastroenterology and Hepatology, 2024, vol. 22, num.4, p. 768-777https://doi.org/10.1016/j.cgh.2023.11.031cc-by (c) Gratacós-Ginès, Jordi et al., 2024http://creativecommons.org/licenses/by/4.0/info:eu-repo/semantics/openAccessoai:recercat.cat:2445/2175352026-05-29T05:05:01Z
dc.title.none.fl_str_mv Alcoholic Foamy Degeneration, an Entity Resembling Alcohol-Associated Hepatitis: Diagnosis, Prognosis, and Molecular Profiling
title Alcoholic Foamy Degeneration, an Entity Resembling Alcohol-Associated Hepatitis: Diagnosis, Prognosis, and Molecular Profiling
spellingShingle Alcoholic Foamy Degeneration, an Entity Resembling Alcohol-Associated Hepatitis: Diagnosis, Prognosis, and Molecular Profiling
Gratacós-Ginès, Jordi
Hepatopaties alcohòliques
Biòpsia
Histologia
Supervivència
Triglicèrids
Alcoholic liver diseases
Biopsy
Histology
Survival
Triglycerides
title_short Alcoholic Foamy Degeneration, an Entity Resembling Alcohol-Associated Hepatitis: Diagnosis, Prognosis, and Molecular Profiling
title_full Alcoholic Foamy Degeneration, an Entity Resembling Alcohol-Associated Hepatitis: Diagnosis, Prognosis, and Molecular Profiling
title_fullStr Alcoholic Foamy Degeneration, an Entity Resembling Alcohol-Associated Hepatitis: Diagnosis, Prognosis, and Molecular Profiling
title_full_unstemmed Alcoholic Foamy Degeneration, an Entity Resembling Alcohol-Associated Hepatitis: Diagnosis, Prognosis, and Molecular Profiling
title_sort Alcoholic Foamy Degeneration, an Entity Resembling Alcohol-Associated Hepatitis: Diagnosis, Prognosis, and Molecular Profiling
dc.creator.none.fl_str_mv Gratacós-Ginès, Jordi
Avitabile, Emma
Montironi, Carla
Guillamon Thiery, Alex
Hernández Évole, Helena
Moreta, Maria José
Blaya, Delia
Ariño, Silvia
Rubio, A.B.
Pérez-Guasch, Martina
Cervera, Marta
Carol, Marta
Fabrellas i Padrès, Núria
Soria, Anna
Juanola Mayos, Adrià
Graupera, Isabel
Sancho-Bru, Pau
Díaz Lorca, Maria Alba
Coll, Mar
Bataller, R.
Ginès i Gibert, Pere
Pose Méndez, Elisa
author Gratacós-Ginès, Jordi
author_facet Gratacós-Ginès, Jordi
Avitabile, Emma
Montironi, Carla
Guillamon Thiery, Alex
Hernández Évole, Helena
Moreta, Maria José
Blaya, Delia
Ariño, Silvia
Rubio, A.B.
Pérez-Guasch, Martina
Cervera, Marta
Carol, Marta
Fabrellas i Padrès, Núria
Soria, Anna
Juanola Mayos, Adrià
Graupera, Isabel
Sancho-Bru, Pau
Díaz Lorca, Maria Alba
Coll, Mar
Bataller, R.
Ginès i Gibert, Pere
Pose Méndez, Elisa
author_role author
author2 Avitabile, Emma
Montironi, Carla
Guillamon Thiery, Alex
Hernández Évole, Helena
Moreta, Maria José
Blaya, Delia
Ariño, Silvia
Rubio, A.B.
Pérez-Guasch, Martina
Cervera, Marta
Carol, Marta
Fabrellas i Padrès, Núria
Soria, Anna
Juanola Mayos, Adrià
Graupera, Isabel
Sancho-Bru, Pau
Díaz Lorca, Maria Alba
Coll, Mar
Bataller, R.
Ginès i Gibert, Pere
Pose Méndez, Elisa
author2_role author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
dc.subject.none.fl_str_mv Hepatopaties alcohòliques
Biòpsia
Histologia
Supervivència
Triglicèrids
Alcoholic liver diseases
Biopsy
Histology
Survival
Triglycerides
topic Hepatopaties alcohòliques
Biòpsia
Histologia
Supervivència
Triglicèrids
Alcoholic liver diseases
Biopsy
Histology
Survival
Triglycerides
description Background & aims: Alcoholic foamy degeneration (AFD) is a condition with similar clinical presentation to alcohol-associated hepatitis (AH), but with a specific histologic pattern. Information regarding the prevalence and prognosis of AFD is scarce and there are no tools for a noninvasive diagnosis. Methods: A cohort of patients admitted to the Hospital Clinic of Barcelona for clinical suspicion of AH who underwent liver biopsy was included. Patients were classified as AFD, AH, or other findings, according to histology. Clinical features, histology, and genetic expression of liver biopsy specimens were analyzed. The accuracy of National Institute on Alcohol Abuse and Alcoholism criteria and laboratory parameters for differential diagnosis were investigated. Results: Of 230 patients with a suspicion of AH, 18 (8%) met histologic criteria for AFD, 184 (80%) had definite AH, and 28 (12%) had other findings. In patients with AFD, massive steatosis was more frequent and the fibrosis stage was lower. AFD was characterized by down-regulation of liver fibrosis and inflammation genes and up-regulation of lipid metabolism and mitochondrial function genes. Patients with AFD had markedly better long-term survival (100% vs 57% in AFD vs AH; P = .002) despite not receiving corticosteroid treatment, even in a model for end-stage liver disease-matched sensitivity analysis. Serum triglyceride levels had an area under the receiver operating characteristic of 0.886 (95% CI, 0.807-0.964) for the diagnosis of AFD, whereas the National Institute on Alcohol Abuse and Alcoholism criteria performed poorly. A 1-step algorithm using triglyceride levels of 225 mg/dL (sensitivity, 0.77; specificity, 0.90; and Youden index, 0.67) is proposed for differential diagnosis. Conclusions: AFD in the setting of suspicion of AH is not uncommon. A differential diagnosis is important because prognosis and treatment differ largely. Triglyceride levels successfully identify most patients with AFD and may be helpful in decision making.
publishDate 2024
dc.date.none.fl_str_mv 2024
2025
2025
2025
dc.type.none.fl_str_mv info:eu-repo/semantics/article
info:eu-repo/semantics/publishedVersion
format article
status_str publishedVersion
dc.identifier.none.fl_str_mv https://hdl.handle.net/2445/217535
url https://hdl.handle.net/2445/217535
dc.language.none.fl_str_mv Inglés
language_invalid_str_mv Inglés
dc.relation.none.fl_str_mv Reproducció del document publicat a: https://doi.org/10.1016/j.cgh.2023.11.031
Clinical Gastroenterology and Hepatology, 2024, vol. 22, num.4, p. 768-777
https://doi.org/10.1016/j.cgh.2023.11.031
dc.rights.none.fl_str_mv cc-by (c) Gratacós-Ginès, Jordi et al., 2024
http://creativecommons.org/licenses/by/4.0/
info:eu-repo/semantics/openAccess
rights_invalid_str_mv cc-by (c) Gratacós-Ginès, Jordi et al., 2024
http://creativecommons.org/licenses/by/4.0/
eu_rights_str_mv openAccess
dc.format.none.fl_str_mv 18 p.
application/pdf
dc.publisher.none.fl_str_mv Elsevier
publisher.none.fl_str_mv Elsevier
dc.source.none.fl_str_mv Articles publicats en revistes (Fonaments Clínics)
reponame:Recercat. Dipósit de la Recerca de Catalunya
instname:Varias* (Consorci de Biblioteques Universitáries de Catalunya, Centre de Serveis Científics i Acadèmics de Catalunya)
instname_str Varias* (Consorci de Biblioteques Universitáries de Catalunya, Centre de Serveis Científics i Acadèmics de Catalunya)
reponame_str Recercat. Dipósit de la Recerca de Catalunya
collection Recercat. Dipósit de la Recerca de Catalunya
repository.name.fl_str_mv
repository.mail.fl_str_mv
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