A Phase II Study of Venetoclax in Combination With Pomalidomide and Dexamethasone in Relapsed/Refractory Multiple Myeloma

© 2021 The Authors.

Detalles Bibliográficos
Autores: Gasparetto, Cristina, Bowles, Kristian M., Abdallah, Al-Ola, Morris, Lura, Mander, Gudrun, Coppola, Sheryl, Wang, J., Ross, J. A., Bueno, Orlando F., Arriola, Emma, Mateos, Maria Victoria
Tipo de recurso: artículo
Estado:Versión publicada
Fecha de publicación:2021
País:España
Institución:Consejo Superior de Investigaciones Científicas (CSIC)
Repositorio:DIGITAL.CSIC. Repositorio Institucional del CSIC
OAI Identifier:oai:digital.csic.es:10261/261010
Acceso en línea:http://hdl.handle.net/10261/261010
Access Level:acceso abierto
Palabra clave:BCL2
Immunomodulatory agents
Plasma cell dyscrasia
Targeted therapy
Venetoclax
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spelling A Phase II Study of Venetoclax in Combination With Pomalidomide and Dexamethasone in Relapsed/Refractory Multiple MyelomaGasparetto, CristinaBowles, Kristian M.Abdallah, Al-OlaMorris, LuraMander, GudrunCoppola, SherylWang, J.Ross, J. A.Bueno, Orlando F.Arriola, EmmaMateos, Maria VictoriaBCL2Immunomodulatory agentsPlasma cell dyscrasiaTargeted therapyVenetoclax© 2021 The Authors.[Background]: Venetoclax is a selective BCL-2 inhibitor with clinical activity in relapsed/refractory multiple myeloma (RRMM). Combinations of venetoclax with agents that have complementary mechanisms of action may improve venetoclax efficacy in RRMM. This study evaluated venetoclax with pomalidomide and dexamethasone (VenPd) in RRMM. [Patients and Methods]: This phase II open label study (NCT03567616) evaluated VenPd in patients with RRMM who had received ≥ 1 prior therapy and were refractory to lenalidomide. Venetoclax was administered orally daily for days 1 to 28, pomalidomide was administered orally daily for days 1 to 21, and dexamethasone was administered weekly for each 28-day cycle. The primary objective was to characterize the safety and tolerability of VenPd. The secondary objectives were to evaluate the efficacy and pharmacokinetics. The study was terminated early due to partial clinical hold and decision to pursue biomarker driven strategy. [Results]: Eight patients were enrolled. Patients had a median age of 67.5 years. All patients received 400 mg venetoclax; 4 patients experienced dose-limiting toxicities and the dose was not escalated. All patients had a grade ≥ 3 adverse event, and the most common was neutropenia (n = 6); cytopenias were the most prevalent adverse events. Five patients (63%) had a confirmed response, and the median duration of response was 12.9 months. The median progression-free survival was 10.5 months. [Conclusions]: Given the limited enrollment, no clear safety or efficacy conclusions about VenPd can be drawn. Preliminary safety data, particularly the occurrence of cytopenias, can be used to guide dosing strategies for future combinations of venetoclax with immunomodulatory agents.AbbVie Inc is a private corporation, and funding is not associated with a grant number. Funding information is correct as stated.ElsevierAbbVie PharmaceuticalsConsejo Superior de Investigaciones Científicas [https://ror.org/02gfc7t72]2022202220212022info:eu-repo/semantics/articlehttp://purl.org/coar/resource_type/c_6501Publisher's versioninfo:eu-repo/semantics/publishedVersionhttp://hdl.handle.net/10261/261010reponame:DIGITAL.CSIC. Repositorio Institucional del CSICinstname:Consejo Superior de Investigaciones Científicas (CSIC)Ingléshttp://dx.doi.org/10.1016/j.clml.2021.07.029Síinfo:eu-repo/semantics/openAccessoai:digital.csic.es:10261/2610102026-05-22T06:33:51Z
dc.title.none.fl_str_mv A Phase II Study of Venetoclax in Combination With Pomalidomide and Dexamethasone in Relapsed/Refractory Multiple Myeloma
title A Phase II Study of Venetoclax in Combination With Pomalidomide and Dexamethasone in Relapsed/Refractory Multiple Myeloma
spellingShingle A Phase II Study of Venetoclax in Combination With Pomalidomide and Dexamethasone in Relapsed/Refractory Multiple Myeloma
Gasparetto, Cristina
BCL2
Immunomodulatory agents
Plasma cell dyscrasia
Targeted therapy
Venetoclax
title_short A Phase II Study of Venetoclax in Combination With Pomalidomide and Dexamethasone in Relapsed/Refractory Multiple Myeloma
title_full A Phase II Study of Venetoclax in Combination With Pomalidomide and Dexamethasone in Relapsed/Refractory Multiple Myeloma
title_fullStr A Phase II Study of Venetoclax in Combination With Pomalidomide and Dexamethasone in Relapsed/Refractory Multiple Myeloma
title_full_unstemmed A Phase II Study of Venetoclax in Combination With Pomalidomide and Dexamethasone in Relapsed/Refractory Multiple Myeloma
title_sort A Phase II Study of Venetoclax in Combination With Pomalidomide and Dexamethasone in Relapsed/Refractory Multiple Myeloma
dc.creator.none.fl_str_mv Gasparetto, Cristina
Bowles, Kristian M.
Abdallah, Al-Ola
Morris, Lura
Mander, Gudrun
Coppola, Sheryl
Wang, J.
Ross, J. A.
Bueno, Orlando F.
Arriola, Emma
Mateos, Maria Victoria
author Gasparetto, Cristina
author_facet Gasparetto, Cristina
Bowles, Kristian M.
Abdallah, Al-Ola
Morris, Lura
Mander, Gudrun
Coppola, Sheryl
Wang, J.
Ross, J. A.
Bueno, Orlando F.
Arriola, Emma
Mateos, Maria Victoria
author_role author
author2 Bowles, Kristian M.
Abdallah, Al-Ola
Morris, Lura
Mander, Gudrun
Coppola, Sheryl
Wang, J.
Ross, J. A.
Bueno, Orlando F.
Arriola, Emma
Mateos, Maria Victoria
author2_role author
author
author
author
author
author
author
author
author
author
dc.contributor.none.fl_str_mv AbbVie Pharmaceuticals
Consejo Superior de Investigaciones Científicas [https://ror.org/02gfc7t72]
dc.subject.none.fl_str_mv BCL2
Immunomodulatory agents
Plasma cell dyscrasia
Targeted therapy
Venetoclax
topic BCL2
Immunomodulatory agents
Plasma cell dyscrasia
Targeted therapy
Venetoclax
description © 2021 The Authors.
publishDate 2021
dc.date.none.fl_str_mv 2021
2022
2022
2022
dc.type.none.fl_str_mv info:eu-repo/semantics/article
http://purl.org/coar/resource_type/c_6501
Publisher's version
info:eu-repo/semantics/publishedVersion
format article
status_str publishedVersion
dc.identifier.none.fl_str_mv http://hdl.handle.net/10261/261010
url http://hdl.handle.net/10261/261010
dc.language.none.fl_str_mv Inglés
language_invalid_str_mv Inglés
dc.relation.none.fl_str_mv http://dx.doi.org/10.1016/j.clml.2021.07.029

dc.rights.none.fl_str_mv info:eu-repo/semantics/openAccess
eu_rights_str_mv openAccess
dc.publisher.none.fl_str_mv Elsevier
publisher.none.fl_str_mv Elsevier
dc.source.none.fl_str_mv reponame:DIGITAL.CSIC. Repositorio Institucional del CSIC
instname:Consejo Superior de Investigaciones Científicas (CSIC)
instname_str Consejo Superior de Investigaciones Científicas (CSIC)
reponame_str DIGITAL.CSIC. Repositorio Institucional del CSIC
collection DIGITAL.CSIC. Repositorio Institucional del CSIC
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