Retinal function in patients with the neuronal ceroid lipofuscinosis phenotype

Purpose: To analyze the clinical features, visual acuity, and full-field electroretinogram (ERG) findings of 15 patients with the neuronal ceroid lipofuscinosis (NCL) phenotype and to establish the role of ERG testing in NCL diagnosis. Methods: The medical records of five patients with infantile NCL...

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Detalles Bibliográficos
Autores: Aparecida Barasnevicius Quagliato, Elizabeth Maria [UNIFESP], Rocha, Daniel Martins [UNIFESP], Sacai, Paula Yuri [UNIFESP], Watanabe, Sung Song [UNIFESP], Salomao, Solange Rios, Berezovsky, Adriana [UNIFESP]
Tipo de recurso: artículo
Estado:Versión publicada
Fecha de publicación:2017
País:Brasil
Institución:Universidade Federal de São Paulo (UNIFESP)
Repositorio:Repositório Institucional da UNIFESP
Idioma:inglés
OAI Identifier:oai:repositorio.unifesp.br:11600/53507
Acceso en línea:https://www.scielo.br/scielo.php?script=sci_arttext&pid=S0004-27492017000400215&lng=en&nrm=iso&tlng=en
https://repositorio.unifesp.br/handle/11600/53507
Access Level:acceso abierto
Palabra clave:Neuronal ceroid lipofuscinoses
Membrane proteins/genetics
Retina/physiopathology
Electroretinography
Retinal dystrophies
Visual acuity
Descripción
Sumario:Purpose: To analyze the clinical features, visual acuity, and full-field electroretinogram (ERG) findings of 15 patients with the neuronal ceroid lipofuscinosis (NCL) phenotype and to establish the role of ERG testing in NCL diagnosis. Methods: The medical records of five patients with infantile NCL, five with Jansky-Bielschowsky disease, and five with juvenile NCL who underwent full-field ERG testing were retrospectively analyzed. Results: Progressive vision loss was the initial symptom in 66.7% of patients and was isolated or associated with ataxia, epilepsy, and neurodevelopmental involution. Epilepsy was present in 93.3% of patients, of whom 86.6% presented with neurodevelopmental involution. Fundus findings ranged from normal to pigmentary/atrophic abnormalities. Cone-rod, rod-cone, and both types of dysfunction were observed in six, one, and eight patients, respectively. Conclusion: In our study, all patients with the NCL phenotype had abnormal ERG findings, and the majority exhibited both cone-rod and rod-cone dysfunction. We conclude that ERG is a valuable tool for the characterization of visual dysfunction in patients with the NCL phenotype and is useful for diagnosis.