Risks of long-term port use in enzyme replacement therapy for lysosomal storage disorders
Totally implantable vascular access devices (TIVADs) are commonly used in conjunction with enzyme replacement therapy (ERT) for lysosomal storage disorders (LSDs). This case series describes potential complications associated with long-term TIVAD use, such as compromise of skin integrity, infection,...
| Autores: | , , , , |
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| Formato: | artículo |
| Estado: | Versión publicada |
| Fecha de publicación: | 2017 |
| País: | Brasil |
| Recursos: | Universidade Federal do Rio Grande do Sul (UFRGS) |
| Repositorio: | Repositório Institucional da UFRGS |
| Idioma: | inglés |
| OAI Identifier: | oai:www.lume.ufrgs.br:10183/196097 |
| Acesso em linha: | http://hdl.handle.net/10183/196097 |
| Access Level: | acceso abierto |
| Palavra-chave: | Mucopolissacaridoses Terapia de reposição de enzimas Dispositivos de acesso vascular Doenças por armazenamento dos lisossomos Mucopolysaccharidosis Enzyme replacement therapy Totally implantable venous access device Lysosomal storage disorder |
| Resumo: | Totally implantable vascular access devices (TIVADs) are commonly used in conjunction with enzyme replacement therapy (ERT) for lysosomal storage disorders (LSDs). This case series describes potential complications associated with long-term TIVAD use, such as compromise of skin integrity, infection, or port failures. Best practices and skilled specialists are essential for minimizing complications from long-term TIVAD use for ERT. |
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