Reliable and cost-effective approach for diagnosis of heterozygous F8/F9 large deletions by quantitative real-time PCR

Haemophilia A (HA) (OMIM#306700) and haemophilia B (HB) (OMIM#306900) are X-linked disorders characterized by deleterious mutations in coagulation factor VIII (F8) and factor IX (F9) genes respectively. Among these mutations, F8 large deletions cause 8-15% of severe HA (www.factorviii-db.org) and F9...

Descripción completa

Detalles Bibliográficos
Autores: Abelleyro, Miguel Martin, Radic, Claudia Pamela, Tetzlaff, Guillermo Tomás, Marchione, Vanina Daniela, Fundia, Ariela Freya, Larripa, Irene Beatriz, Rossetti, Liliana Carmen, de Brasi, Carlos Daniel
Tipo de recurso: artículo
Estado:Versión publicada
Fecha de publicación:2015
País:Argentina
Institución:Consejo Nacional de Investigaciones Científicas y Técnicas
Repositorio:CONICET Digital (CONICET)
Idioma:inglés
OAI Identifier:oai:ri.conicet.gov.ar:11336/38532
Acceso en línea:http://hdl.handle.net/11336/38532
Access Level:acceso abierto
Palabra clave:Hemofilia
Grandes Deleciones Heterocigotas
Genes F8 y F9
Diagnóstico Molecular
https://purl.org/becyt/ford/3.1
https://purl.org/becyt/ford/3
Descripción
Sumario:Haemophilia A (HA) (OMIM#306700) and haemophilia B (HB) (OMIM#306900) are X-linked disorders characterized by deleterious mutations in coagulation factor VIII (F8) and factor IX (F9) genes respectively. Among these mutations, F8 large deletions cause 8-15% of severe HA (www.factorviii-db.org) and F9 large deletions 6-13% of severe HB (www.factorix.org/). Molecular diagnosis of F8 or F9 large deletions (F8/F9-LDs) is critically important because these mutations associate with a highly significant predisposition to develop inhibitors against exogenous FVIII or FIX, the most troublesome complication for haemophilia treatment.