Timely diagnosis of Wilson's disease using whole exome sequencing

Wilson's disease (WD) is a rare inborn error of copper metabolism caused by mutations in ATP7B gene. Although there is no genetic heterogeneity in WD etiology, the widespread clinical presentation of WD makes its diagnosis not always straightforward, particularly when atypical symptoms are pres...

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Detalles Bibliográficos
Autores: Rodríguez Quiroga, Sergio Alejandro, Rosales, Julieta, Arakaki, Tomoko, Córdoba, Marta, Gonzalez Moron, Dolores, Medina, Nancy, Garreto, Nélida S., Kauffman, Marcelo Andres
Tipo de recurso: artículo
Estado:Versión publicada
Fecha de publicación:2015
País:Argentina
Institución:Consejo Nacional de Investigaciones Científicas y Técnicas
Repositorio:CONICET Digital (CONICET)
Idioma:inglés
OAI Identifier:oai:ri.conicet.gov.ar:11336/17745
Acceso en línea:http://hdl.handle.net/11336/17745
Access Level:acceso abierto
Palabra clave:Wilson'S Disease
Neurogenetics
Atp7b Gene
Next-Generation-Sequencing
Exome Sequencing
https://purl.org/becyt/ford/3.2
https://purl.org/becyt/ford/3
Descripción
Sumario:Wilson's disease (WD) is a rare inborn error of copper metabolism caused by mutations in ATP7B gene. Although there is no genetic heterogeneity in WD etiology, the widespread clinical presentation of WD makes its diagnosis not always straightforward, particularly when atypical symptoms are present and a number of differential diagnoses must be considered.