Increased delivery of chemotherapy to the vitreous by inhibition of the blood-retinal barrier

Treatment of retinoblastoma -a pediatric cancer of the developing retina- might benefit from strategies to inhibit the blood-retinal barrier (BRB). The potent anticancer agent topotecan is a substrate of efflux transporters BCRP and P-gp, which are expressed at the BRB to restrict vitreous and retin...

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Detalles Bibliográficos
Autores: Pascual-Pasto, Guillem, Olaciregui, Nagore G., Opezzo, Javier A. W., Castillo Ecija, Helena, Cuadrado Vilanova, Maria, Paco, Sonia, Rivero, Ezequiel Mariano, Vila Ubach, Monica, Restrepo Perdomo, Camilo A., Torrebadell, Montserrat, Suñol, Mariona, Schaiquevich, Paula Susana, Mora, Jaume, Bramuglia, Guillermo Federico, Chantada, Guillermo Luis, Carcaboso, Angel M.
Tipo de recurso: artículo
Estado:Versión publicada
Fecha de publicación:2017
País:Argentina
Institución:Consejo Nacional de Investigaciones Científicas y Técnicas
Repositorio:CONICET Digital (CONICET)
Idioma:inglés
OAI Identifier:oai:ri.conicet.gov.ar:11336/85225
Acceso en línea:http://hdl.handle.net/11336/85225
Access Level:acceso abierto
Palabra clave:ABC TRANSPORTERS
ABCB1/P-GP
ABCG2/BCRP
BCRP
BLOOD-RETINAL BARRIER
DELIVERY
DISTRIBUTION
MICRODIALYSIS
P-GP
PANTOPRAZOLE
PEDIATRIC CANCER
RABBIT
RETINA
RETINOBLASTOMA
TOPOTECAN
VITREOUS
XENOGRAFT
https://purl.org/becyt/ford/3.1
https://purl.org/becyt/ford/3
Descripción
Sumario:Treatment of retinoblastoma -a pediatric cancer of the developing retina- might benefit from strategies to inhibit the blood-retinal barrier (BRB). The potent anticancer agent topotecan is a substrate of efflux transporters BCRP and P-gp, which are expressed at the BRB to restrict vitreous and retinal distribution of xenobiotics. In this work we have studied vitreous and retinal distribution, tumor accumulation and antitumor activity of topotecan, using pantoprazole as inhibitor of BCRP and P-gp. We used rabbit and mouse eyes as BRB models and patient-derived xenografts as retinoblastoma models. To validate the rabbit BRB model we stained BCRP and P-gp in the retinal vessels. Using intravitreous microdialysis we showed that the penetration of the rabbit vitreous by lactone topotecan increased significantly upon concomitant administration of pantoprazole (P = 0.0285). Pantoprazole also increased topotecan penetration of the mouse vitreous, measured as the vitreous-to-plasma topotecan concentration ratio at the steady state (P = 0.0246). Pantoprazole increased topotecan antitumor efficacy and intracellular penetration in retinoblastoma in vitro, but did not enhance intratumor drug distribution and survival in mice bearing the intraocular human tumor HSJD-RBT-2. Anatomical differences with the clinical setting likely limited our in vivo study, since xenografts were poorly vascularized masses that loaded most of the vitreous compartment. We conclude that pharmacological modulation of the BRB is feasible, enhances anticancer drug distribution into the vitreous and might have clinical implications in retinoblastoma.