siRNA modified with 2′-deoxy-2′-c-methylpyrimidine nucleosides

(2′S)-2′-Deoxy-2′-C-methyluridine and (2′R)-2′-deoxy-2′-C-meth-yluridine were incorporated in the 3’-overhang region of the sense and antisense strands and in positions 2 and 5 of the seed region of siRNA duplexes directed against Renilla luciferase, whereas (2′S)-2′-deoxy-2′-C-methylcytidine was in...

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Detalhes bibliográficos
Autores: Dellafiore, María Andrea, Aviñó, Anna, Alagia, Adele, Montserrat, Javier Marcelo, Iribarren, Adolfo Marcelo, Eritja, Ramon
Formato: artículo
Estado:Versión publicada
Fecha de publicación:2018
País:Argentina
Recursos:Consejo Nacional de Investigaciones Científicas y Técnicas
Repositorio:CONICET Digital (CONICET)
Idioma:inglés
OAI Identifier:oai:ri.conicet.gov.ar:11336/98721
Acesso em linha:http://hdl.handle.net/11336/98721
Access Level:acceso abierto
Palavra-chave:ACTIVITY RELATIONSHIPS
DEOXYMETHYLPYRIMIDINE BASES
NUCLEOSIDES
SIRNA
STABILITY
STRUCTURE
https://purl.org/becyt/ford/1.4
https://purl.org/becyt/ford/1
Descrição
Resumo:(2′S)-2′-Deoxy-2′-C-methyluridine and (2′R)-2′-deoxy-2′-C-meth-yluridine were incorporated in the 3’-overhang region of the sense and antisense strands and in positions 2 and 5 of the seed region of siRNA duplexes directed against Renilla luciferase, whereas (2′S)-2′-deoxy-2′-C-methylcytidine was incorporated in the 6-position of the seed region of the same constructions. A dual luciferase reporter assay in transfected HeLa cells was used as a model system to measure the IC50 values of 24 different modified duplexes. The best results were obtained by the substitution of one thymidine unit in the antisense 3’-overhang region by (2′S)-or (2′R)-2′-deoxy-2′-C-methyluridine, reducing IC50 to half of the value observed for the natural control. The selectivity of the modified siRNA was measured, it being found that modifications in positions 5 and 6 of the seed region had a positive effect on the ON/OFF activity.